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庞贝氏症市场，按给药途径、最终用途、治疗类型、国家和地区 - 2023-2030 年行业分析、市场规模、市场份额和预测
市场调查报告书
商品编码
1351405

庞贝氏症市场，按给药途径、最终用途、治疗类型、国家和地区 - 2023-2030 年行业分析、市场规模、市场份额和预测

Pompe Disease Market, By Route of Administration, By End-Use, By Treatment Type, By Country, and By Region - Industry Analysis, Market Size, Market Share & Forecast from 2023-2030
出版日期: | 出版商: AnalystView Market Insights | 英文 290 Pages | 商品交期: 2-3个工作天内

价格

报告要点

2022 年庞贝氏症市场规模为 13.2223 亿美元，2023 年至 2030 年复合年增长率为 4.2%。

庞贝氏症市场 - 市场动态：

  • 製药公司、研究机构和患者权益团体之间不断加强合作，以推动市场需求
  • 致力于庞贝氏症患者的製药公司、学术机构和倡导组织之间不断加强的合作极大地推动了庞贝氏症研究和治疗的进步。这种协作协同作用促进了知识、专业知识和资源的交流，从而加快了创新疗法的发现。监管机构提供奖励措施和孤儿药称号，以激励公司投资于罕见疾病研究。此外，患者权益团体透过提高公众意识和组织筹款活动为研究和临床试验筹集资金，发挥关键作用。这项集体努力增强了我们对该疾病根本原因的了解，并为个人化治疗的发展铺平了道路，最终改善了庞贝氏症患者的预后和生活品质。

庞贝氏症市场 - 主要见解：

  • 我们的研究分析师估计，在2023 年至2030 年的预测期内，全球庞贝氏症市场的年复合成长率预计约为4.2%。这一预期成长归因于製药公司、研究机构和患者倡议之间不断加强的合作小组，显示推进庞贝氏症研究和治疗的正面趋势。
  • 全球庞贝氏症市场根据各种因素进行分类，包括给药途径、最终用途和地区。
  • 在给药途径类别中，肠外给药在 2022 年成为主导部分。这表明在治疗庞贝氏症时对这种给药方式的显着偏好。
  • 在最终用途细分方面，医院在 2022 年处于领先地位。这表明医院在为庞贝病患者提供医疗护理和治疗方面发挥着至关重要的作用。
  • 此外，北美成为 2022 年不同地区的主要收入来源。

庞贝氏症市场-細項分析：

  • 全球庞贝氏症市场根据各种因素进行细分，包括给药途径、最终用途、治疗类型和地区。
  • 在给药途径确定的类别中，注射剂领域占据市场主导地位。这显示在治疗庞贝氏症（一种罕见的遗传性疾病）时普遍偏好肠外治疗。透过静脉注射进行酵素替代疗法（ERT）在疾病管理中发挥关键作用。这种疗法直接输送缺乏的酶，有效解决细胞内肝醣累积的问题，进而改善受影响个体的肌肉功能。

庞贝氏症市场-竞争格局：

庞贝氏症研究和治疗领域的特点是製药公司、研究机构和倡导团体之间的动态交互作用。与学术组织的合作促进了科学进步，而患者倡导团体在提高意识、资助研究工作和倡导监管支持方面发挥关键作用。孤儿药资格进一步激励了该领域的竞争。在这个竞争环境中，公司透过强调治疗效果、可及性和患者支持计划的实施来努力使自己脱颖而出。这项竞赛是加速进步的催化剂，带来更广泛的治疗选择，并全面提高为庞贝氏症患者提供的照护品质。

最近的发展：

2023 年 6 月，Amicus Therapeutics 是一家面向全球的生物技术公司，以患者为中心，专门从事罕见疾病创新药物的开发和商业化，宣布了一个重要的里程碑。欧盟委员会 (EC) 批准 Opfolda (miglustat) 65 毫克胶囊（一种西帕葡萄糖苷酶 alfa 的酶稳定剂）作为患有晚发性庞贝氏症的成年人的长期酶替代疗法。

目录

第 1 章：庞贝氏症市场概述

  • 研究范围
  • 市场预估年份

第 2 章：执行摘要

  • 市场片段
    • 按给药途径分類的庞贝氏症市场片段
    • 按治疗类型分類的庞贝氏症市场片段
    • 最终用户的庞贝氏症市场片段
    • 庞贝氏症市场片段（按国家/地区）
    • 按地区分類的庞贝氏症市场片段
  • 竞争洞察

第 3 章：庞贝氏症主要市场趋势

  • 庞贝氏症市场驱动因素
    • 市场驱动因素的影响分析
  • 庞贝氏症市场限制
    • 市场限制影响分析
  • 庞贝氏症市场机会
  • 庞贝氏症市场未来趋势

第 4 章：庞贝氏症产业研究

  • PEST分析
  • 波特五力分析
  • 成长前景图
  • 规范架构分析

第 5 章：庞贝氏症市场：COVID-19 影响分析

  • COVID-19 之前的影响分析
  • COVID-19 后影响分析
    • 表现最佳的市场区隔
    • 边际增长部分
    • 最鬆散的部分
    • 边际损失部分

第 6 章：庞贝氏症市场格局

  • 2022 年庞贝氏症市场占有率分析
  • 按主要製造商分類的故障数据
    • 既定玩家分析
    • 新兴玩家分析

第 7 章：庞贝氏症市场 - 按给药途径

  • 概述
    • 按给药途径分類的细分市占率分析
    • 口服
    • 注射用

第 8 章：庞贝氏症市场 - 按治疗类型

  • 概述
    • 按治疗类型分類的细分市场份额分析
    • 底物减少疗法（SRT）
    • 酵素替代疗法（ERT）
    • 其他

第 9 章：庞贝氏症市场 - 按最终用户

  • 概述
    • 按最终用户分類的细分市场占有率分析
    • 医院
    • 门诊手术中心
    • 其他

第 10 章：庞贝氏症市场 - 按地理位置

  • 介绍
    • 按地理位置分類的细分市场占有率分析
  • 北美洲
    • 概述
    • 庞贝氏症北美主要製造商
    • 北美市场规模和预测（按国家）
    • 北美市场规模与预测（按管理途径）
    • 北美市场规模和预测（按治疗类型）
    • 北美市场规模和预测（按最终用户）
    • 我们
    • 加拿大
  • 欧洲
    • 概述
    • 庞贝氏病欧洲主要製造商
    • 欧洲市场规模和预测（按国家）
    • 欧洲市场规模与预测（按管理途径）
    • 欧洲市场规模和预测（按治疗类型）
    • 欧洲市场规模和预测（按最终用户）
    • 德国
    • 义大利
    • 英国
    • 法国
    • 俄罗斯
    • 荷兰
    • 瑞典
    • 波兰
    • 欧洲其他地区
  • 亚太地区 (APAC)
    • 概述
    • 庞贝氏症亚太地区主要製造商
    • 亚太地区市场规模与预测（按国家）
    • 亚太地区市场规模与预测（依管理途径）
    • 亚太地区市场规模与预测（按治疗类型）
    • 亚太地区市场规模和预测（按最终用户）
    • 印度
    • 中国
    • 日本
    • 韩国
    • 澳洲
    • 泰国
    • 印尼
    • 菲律宾
    • 亚太地区其他地区
  • 拉丁美洲
    • 概述
    • 拉丁美洲庞贝氏症主要製造商
    • 拉丁美洲市场规模与预测（按国家）
    • 拉丁美洲市场规模与预测（按管理途径）
    • 拉丁美洲市场规模与预测（按治疗类型）
    • 拉丁美洲市场规模和预测（按最终用户）
    • 巴西
    • 墨西哥
    • 阿根廷
    • 哥伦比亚
    • 拉丁美洲其他地区
  • 中东和非洲
    • 概述
    • 中东和非洲庞贝病主要製造商
    • 中东和非洲市场规模及预测（按国家）
    • 中东和非洲市场规模及预测（按管理途径）
    • 中东和非洲市场规模及预测（按治疗类型）
    • 中东和非洲市场规模和预测（按最终用户）
    • 沙乌地阿拉伯
    • 阿拉伯聯合大公国
    • 以色列
    • 土耳其
    • 阿尔及利亚
    • 埃及
    • MEA 的其余部分

第 11 章：主要供应商分析 - 庞贝氏症产业

  • 竞争仪表板
  • 公司简介
    • Sanofi Genzyme
    • Amicus Therapeutics
    • BioMarin Pharmaceutical
    • Ultragenyx Pharmaceutical
    • Audentes Therapeutics
    • Avrobio
    • Regenxbio
    • EpiVax
    • Selecta Biosciences
    • Cytokinetics
    • Adverum Biotechnologies
    • Audentes Therapeutics
    • JCR Pharmaceuticals
    • Audentes Therapeutics
    • Valerion Therapeutics

第 12 章：360 度分析师视角

第 13 章：附录

  • 研究方法论
  • 参考
  • 缩写
  • 免责声明
  • 联络我们
Product Code: ANV1642

REPORT HIGHLIGHT

Pompe Disease Market size was valued at USD 1,322.23 Million in 2022, expanding at a CAGR of 4.2% from 2023 to 2030.

Pompe disease, a rare genetic disorder, arises from a deficiency of the enzyme acid alpha-glucosidase (GAA). This deficiency leads to the accumulation of glycogen within cells, with the most pronounced impact on muscle tissues, resulting in a gradual loss of function. Symptoms commonly associated with this condition encompass muscle weakness, respiratory challenges, and cardiac complications. The disease's severity varies, with some individuals experiencing early-onset forms that can have life-threatening cardiac and muscular consequences, while others may have a later onset characterized primarily by muscle weakening. Pompe disease underscores the crucial importance of early detection and ongoing medical management to mitigate its impact on an individual's overall quality of life.

Pompe Disease Market - Market Dynamics:

  • Growing collaboration between pharmaceutical companies, research institutions, and patient advocacy groups to propel market demand
  • The advancement of research and treatment for Pompe disease is significantly propelled by the increasing collaboration among pharmaceutical companies, academic institutions, and advocacy organizations dedicated to patients with this condition. This collaborative synergy facilitates the exchange of knowledge, expertise, and resources, thereby expediting the discovery of innovative therapies. Regulatory bodies provide incentives and orphan drug designations to incentivize companies to invest in rare disease research. Additionally, patient advocacy groups play a pivotal role by raising public awareness and organizing fundraising initiatives that generate funds for research and clinical trials. This collective endeavor enhances our understanding of the disease's underlying causes and paves the way for the development of personalized treatments, ultimately improving the prognosis and quality of life for individuals affected by Pompe disease.

Pompe Disease Market - Key Insights:

  • Our research analyst estimates that the global Pompe Disease market is poised for annual growth at a CAGR of approximately 4.2% during the forecast period from 2023 to 2030. This projected growth is attributed to the increasing collaboration among pharmaceutical firms, research institutions, and patient advocacy groups, indicating a positive trend toward advancing Pompe Disease research and treatment.
  • The Global Pompe Disease Market is categorized based on various factors, including Route of Administration, End-Use, and Region.
  • Within the Route of Administration category, Parenteral administration stood out as the dominant segment in the year 2022. This indicates a significant preference for this mode of administration in treating Pompe Disease.
  • In terms of End-Use segmentation, Hospitals took the lead in 2022. This suggests that hospitals play a crucial role in providing medical care and treatment for Pompe Disease patients.
  • Moreover, North America emerged as the primary revenue generator in 2022 among different regions.

Pompe Disease Market- Segmentation Analysis:

  • The Global Pompe Disease Market presents segmentation based on various factors, including Route of Administration, End-Use, Treatment Type, and Region.
  • Among the categories determined by Route of Administration, the Parenteral sector takes the lead in market dominance. This indicates a prevalent preference for parenteral treatments in managing Pompe disease, a rare genetic disorder. The administration of enzyme replacement therapy (ERT) through intravenous injections plays a pivotal role in disease management. This therapy directly delivers the deficient enzyme, effectively addressing glycogen accumulation within cells, and thereby improving muscle function in affected individuals.

Pompe Disease Market- Competitive Landscape:

The landscape of Pompe disease research and treatment is characterized by a dynamic interplay among pharmaceutical companies, research institutions, and advocacy groups. Collaborative efforts with academic organizations foster scientific advancements, while patient advocacy groups play a pivotal role in raising awareness, funding research endeavors, and advocating for regulatory support. The orphan drug designation further incentivizes competitiveness within the field. In this competitive environment, companies strive to set themselves apart by emphasizing treatment efficacy, accessibility, and the implementation of patient support initiatives. This competition acts as a catalyst for accelerated progress, leading to a broader range of therapeutic options and an overall enhancement in the quality of care provided to individuals with Pompe disease.

Recent Developments:

In June 2023, Amicus Therapeutics, a globally oriented biotechnology firm with a patient-centered approach, specializing in the development and commercialization of innovative medications for rare diseases, announced a significant milestone. The European Commission (EC) granted approval for Opfolda (miglustat) 65mg capsules, an enzyme stabilizer for cipaglucosidase alfa, as a long-term enzyme replacement therapy for adults afflicted with late-onset Pompe disease.

SCOPE OF THE REPORT

The scope of this report covers the market by its major segments, which include as follows:

GLOBAL POMPE DISEASE MARKET KEY PLAYERS

  • Sanofi Genzyme
  • Amicus Therapeutics
  • BioMarin Pharmaceutical
  • Ultragenyx Pharmaceutical
  • Audentes Therapeutics
  • Avrobio
  • Regenxbio
  • EpiVax
  • Selecta Biosciences
  • Cytokinetics
  • Adverum Biotechnologies
  • Audentes Therapeutics
  • JCR Pharmaceuticals
  • Audentes Therapeutics
  • Valerion Therapeutics

GLOBAL POMPE DISEASE MARKET, BY ROUTE OF ADMINISTRATION

  • Oral
  • Parenteral

GLOBAL POMPE DISEASE MARKET, BY END-USE

  • Hospitals
  • Ambulatory Surgical Centers
  • Other

GLOBAL POMPE DISEASE MARKET, BY TREATMENT TYPE

  • Substrate Reduction Therapy (SRT)
  • Enzyme Replacement Therapy (ERT)
  • Other

GLOBAL POMPE DISEASE MARKET, BY REGION

  • North America
    • The U.S.
    • Canada
  • Europe
    • Germany
    • France
    • Italy
    • Spain
    • United Kingdom
    • Russia
    • Netherlands
    • Sweden
    • Poland
    • Rest of Europe
  • Asia Pacific
    • India
    • China
    • South Korea
    • Japan
    • Australia
    • Thailand
    • Indonesia
    • Philippines
    • Rest of APAC
  • Latin America
    • Brazil
    • Mexico
    • Argentina
    • Colombia
    • Rest of LATAM
  • The Middle East and Africa
    • Saudi Arabia
    • United Arab Emirates
    • Israel
    • Turkey
    • Algeria
    • Egypt
    • Rest of MEA

Table of Contents

1. Pompe Disease Market Overview

  • 1.1. Study Scope
  • 1.2. Market Estimation Years

2. Executive Summary

  • 2.1. Market Snippet
    • 2.1.1. Pompe Disease Market Snippet by Route of Administration
    • 2.1.2. Pompe Disease Market Snippet by Treatment Type
    • 2.1.3. Pompe Disease Market Snippet by End-User
    • 2.1.4. Pompe Disease Market Snippet by Country
    • 2.1.5. Pompe Disease Market Snippet by Region
  • 2.2. Competitive Insights

3. Pompe Disease Key Market Trends

  • 3.1. Pompe Disease Market Drivers
    • 3.1.1. Impact Analysis of Market Drivers
  • 3.2. Pompe Disease Market Restraints
    • 3.2.1. Impact Analysis of Market Restraints
  • 3.3. Pompe Disease Market Opportunities
  • 3.4. Pompe Disease Market Future Trends

4. Pompe Disease Industry Study

  • 4.1. PEST Analysis
  • 4.2. Porter's Five Forces Analysis
  • 4.3. Growth Prospect Mapping
  • 4.4. Regulatory Framework Analysis

5. Pompe Disease Market: COVID-19 Impact Analysis

  • 5.1. Pre-COVID-19 Impact Analysis
  • 5.2. Post-COVID-19 Impact Analysis
    • 5.2.1. Top Performing Segments
    • 5.2.2. Marginal Growth Segments
    • 5.2.3. Top Looser Segments
    • 5.2.4. Marginal Loss Segments

6. Pompe Disease Market Landscape

  • 6.1. Pompe Disease Market Share Analysis, 2022
  • 6.2. Breakdown Data, by Key Manufacturer
    • 6.2.1. Established Players' Analysis
    • 6.2.2. Emerging Players' Analysis

7. Pompe Disease Market - By Route of Administration

  • 7.1. Overview
    • 7.1.1. Segment Share Analysis, By Route of Administration, 2022 & 2030 (%)
    • 7.1.2. Oral
    • 7.1.3. Parenteral

8. Pompe Disease Market - By Treatment Type

  • 8.1. Overview
    • 8.1.1. Segment Share Analysis, By Treatment Type, 2022 & 2030 (%)
    • 8.1.2. Substrate Reduction Therapy (SRT)
    • 8.1.3. Enzyme Replacement Therapy (ERT)
    • 8.1.4. Other

9. Pompe Disease Market - By End-User

  • 9.1. Overview
    • 9.1.1. Segment Share Analysis, By End-User, 2022 & 2030 (%)
    • 9.1.2. Hospitals
    • 9.1.3. Ambulatory Surgical Centers
    • 9.1.4. Other

10. Pompe Disease Market- By Geography

  • 10.1. Introduction
    • 10.1.1. Segment Share Analysis, By Geography, 2022 & 2030 (%)
  • 10.2. North America
    • 10.2.1. Overview
    • 10.2.2. Pompe Disease Key Manufacturers in North America
    • 10.2.3. North America Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.2.4. North America Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.2.5. North America Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.2.6. North America Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.2.7. U.S.
      • 10.2.7.1. Overview
      • 10.2.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.2.7.3. U.S. Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.2.7.4. U.S. Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.2.7.5. U.S. Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.2.8. Canada
      • 10.2.8.1. Overview
      • 10.2.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.2.8.3. Canada Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.2.8.4. Canada Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.2.8.5. Canada Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.3. Europe
    • 10.3.1. Overview
    • 10.3.2. Pompe Disease Key Manufacturers in Europe
    • 10.3.3. Europe Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.3.4. Europe Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.3.5. Europe Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.3.6. Europe Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.7. Germany
      • 10.3.7.1. Overview
      • 10.3.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.7.3. Germany Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.7.4. Germany Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.7.5. Germany Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.8. Italy
      • 10.3.8.1. Overview
      • 10.3.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.8.3. Italy Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.8.4. Italy Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.8.5. Italy Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.9. United Kingdom
      • 10.3.9.1. Overview
      • 10.3.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.9.3. United Kingdom Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.9.4. United Kingdom Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.9.5. United Kingdom Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.10. France
      • 10.3.10.1. Overview
      • 10.3.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.10.3. France Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.10.4. France Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.10.5. France Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.11. Russia
      • 10.3.11.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.11.2. Russia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.11.3. Russia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.11.4. Russia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.12. Netherlands
      • 10.3.12.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.12.2. Netherlands Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.12.3. Netherlands Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.12.4. Netherlands Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.13. Sweden
      • 10.3.13.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.13.2. Sweden Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.13.3. Sweden Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.13.4. Sweden Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.14. Poland
      • 10.3.14.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.14.2. Poland Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.14.3. Poland Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.14.4. Poland Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.15. Rest of Europe
      • 10.3.15.1. Overview
      • 10.3.15.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.15.3. Rest of the Europe Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.15.4. Rest of the Europe Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.15.5. Rest of the Europe Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.4. Asia Pacific (APAC)
    • 10.4.1. Overview
    • 10.4.2. Pompe Disease Key Manufacturers in Asia Pacific
    • 10.4.3. Asia Pacific Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.4.4. Asia Pacific Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.4.5. Asia Pacific Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.4.6. Asia Pacific Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.7. India
      • 10.4.7.1. Overview
      • 10.4.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.7.3. India Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.7.4. India Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.7.5. India Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.8. China
      • 10.4.8.1. Overview
      • 10.4.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.8.3. China Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.8.4. China Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.8.5. China Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.9. Japan
      • 10.4.9.1. Overview
      • 10.4.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.9.3. Japan Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.9.4. Japan Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.9.5. Japan Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.10. South Korea
      • 10.4.10.1. Overview
      • 10.4.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.10.3. South Korea Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.10.4. South Korea Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.10.5. South Korea Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.11. Australia
      • 10.4.11.1. Overview
      • 10.4.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.11.3. Australia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.11.4. Australia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.11.5. Australia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.12. Thailand
      • 10.4.12.1. Overview
      • 10.4.12.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.12.3. Thailand Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.12.4. Thailand Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.12.5. Thailand Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.13. Indonesia
      • 10.4.13.1. Overview
      • 10.4.13.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.13.3. Indonesia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.13.4. Indonesia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.13.5. Indonesia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.14. Philippines
      • 10.4.14.1. Overview
      • 10.4.14.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.14.3. Philippines Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.14.4. Philippines Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.14.5. Philippines Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.15. Rest of APAC
      • 10.4.15.1. Overview
      • 10.4.15.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.15.3. Rest of APAC Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.15.4. Rest of APAC Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.15.5. Rest of APAC Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.5. Latin America
    • 10.5.1. Overview
    • 10.5.2. Pompe Disease Key Manufacturers in Latin America
    • 10.5.3. Latin America Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.5.4. Latin America Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.5.5. Latin America Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.5.6. Latin America Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.7. Brazil
      • 10.5.7.1. Overview
      • 10.5.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.7.3. Brazil Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.7.4. Brazil Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.7.5. Brazil Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.8. Mexico
      • 10.5.8.1. Overview
      • 10.5.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.8.3. Mexico Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.8.4. Mexico Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.8.5. Mexico Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.9. Argentina
      • 10.5.9.1. Overview
      • 10.5.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.9.3. Argentina Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.9.4. Argentina Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.9.5. Argentina Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.10. Colombia
      • 10.5.10.1. Overview
      • 10.5.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.10.3. Colombia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.10.4. Colombia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.10.5. Colombia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.11. Rest of LATAM
      • 10.5.11.1. Overview
      • 10.5.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.11.3. Rest of LATAM Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.11.4. Rest of LATAM Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.11.5. Rest of LATAM Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.6. Middle East and Africa
    • 10.6.1. Overview
    • 10.6.2. Pompe Disease Key Manufacturers in Middle East and Africa
    • 10.6.3. Middle East and Africa Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.6.4. Middle East and Africa Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.6.5. Middle East and Africa Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.6.6. Middle East and Africa Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.7. Saudi Arabia
      • 10.6.7.1. Overview
      • 10.6.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.7.3. Saudi Arabia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.7.4. Saudi Arabia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.7.5. Saudi Arabia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.8. United Arab Emirates
      • 10.6.8.1. Overview
      • 10.6.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.8.3. United Arab Emirates Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.8.4. United Arab Emirates Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.8.5. United Arab Emirates Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.9. Israel
      • 10.6.9.1. Overview
      • 10.6.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.9.3. Israel Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.9.4. Israel Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.9.5. Israel Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.10. Turkey
      • 10.6.10.1. Overview
      • 10.6.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.10.3. Turkey Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.10.4. Turkey Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.10.5. Turkey Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.11. Algeria
      • 10.6.11.1. Overview
      • 10.6.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.11.3. Algeria Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.11.4. Algeria Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.11.5. Algeria Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.12. Egypt
      • 10.6.12.1. Overview
      • 10.6.12.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.12.3. Egypt Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.12.4. Egypt Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.12.5. Egypt Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.13. Rest of MEA
      • 10.6.13.1. Overview
      • 10.6.13.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.13.3. Rest of MEA Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.13.4. Rest of MEA Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.13.5. Rest of MEA Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)

11. Key Vendor Analysis- Pompe Disease Industry

  • 11.1. Competitive Dashboard
  • 11.2. Company Profiles
    • 11.2.1. Sanofi Genzyme
    • 11.2.2. Amicus Therapeutics
    • 11.2.3. BioMarin Pharmaceutical
    • 11.2.4. Ultragenyx Pharmaceutical
    • 11.2.5. Audentes Therapeutics
    • 11.2.6. Avrobio
    • 11.2.7. Regenxbio
    • 11.2.8. EpiVax
    • 11.2.9. Selecta Biosciences
    • 11.2.10. Cytokinetics
    • 11.2.11. Adverum Biotechnologies
    • 11.2.12. Audentes Therapeutics
    • 11.2.13. JCR Pharmaceuticals
    • 11.2.14. Audentes Therapeutics
    • 11.2.15. Valerion Therapeutics

12. 360 Degree Analyst View

13. Appendix

  • 13.1. Research Methodology
  • 13.2. References
  • 13.3. Abbreviations
  • 13.4. Disclaimer
  • 13.5. Contact Us

List of Tables

  • TABLE List of data sources
  • TABLE Market drivers; Impact Analysis
  • TABLE Market restraints; Impact Analysis
  • TABLE Pompe Disease Market: Route of Administration Snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by Route of Administration
  • TABLE Global Pompe Disease Market, by Route of Administration 2018-2030 (USD Million)
  • TABLE Pompe Disease Market: Treatment Type Snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by Treatment Type
  • TABLE Global Pompe Disease Market, by Treatment Type 2018-2030 (USD Million)
  • TABLE Pompe Disease Market: End-User Snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by End-User
  • TABLE Global Pompe Disease Market, by End-User 2018-2030 (USD Million)
  • TABLE Pompe Disease Market: Regional snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by Region
  • TABLE Global Pompe Disease Market, by Region 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by End-User, 2018-2030 (USD Million)

List of Figures

  • FIGURE Pompe Disease Market Segmentation
  • FIGURE Market research methodology
  • FIGURE Value chain analysis
  • FIGURE Porter's Five Forces Analysis
  • FIGURE Market Attractiveness Analysis
  • FIGURE COVID-19 Impact Analysis
  • FIGURE Pre & Post COVID-19 Impact Comparision Study
  • FIGURE Competitive Landscape; Key company market share analysis, 2022
  • FIGURE Route of Administration segment market share analysis, 2022 & 2030
  • FIGURE Route of Administration segment market size forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Treatment Type segment market share analysis, 2022 & 2030
  • FIGURE Treatment Type segment market size forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE End-User segment market share analysis, 2022 & 2030
  • FIGURE End-User segment market size forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Regional segment market share analysis, 2022 & 2030
  • FIGURE Regional segment market size forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE North America Pompe Disease Market share and leading players, 2022
  • FIGURE Europe Pompe Disease Market share and leading players, 2022
  • FIGURE Asia Pacific Pompe Disease Market share and leading players, 2022
  • FIGURE Latin America Pompe Disease Market share and leading players, 2022
  • FIGURE Middle East and Africa Pompe Disease Market share and leading players, 2022
  • FIGURE North America market share analysis by country, 2022
  • FIGURE U.S. Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Canada Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Europe Pompe Disease Market share analysis by country, 2022
  • FIGURE Germany Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Spain Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Italy Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE France Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE UK Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Russia Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Netherlands Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Sweden Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Poland Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Rest of the Europe Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Asia Pacific Pompe Disease Market share analysis by country, 2022
  • FIGURE India Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE China Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Japan Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE South Korea Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Australia Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Thailand Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Indonesia Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Phillipines Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Rest of APAC Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Latin America Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Latin America Pompe Disease Market share analysis by country, 2022
  • FIGURE Brazil Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Mexico Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Argentina Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Colombia Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Rest of LATAM Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Middle East and Africa Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Middle East and Africa Pompe Disease Market share analysis by country, 2022
  • FIGURE Saudi Arabia Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE United Arab Emirates Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Israel Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Turkey Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Algeria Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Egypt Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)
  • FIGURE Rest of MEA Pompe Disease Market size, forecast and trend analysis, 2018 to 2030 (USD Million)