封面
市场调查报告书
商品编码
1567164

巴斯症候群治疗市场:依治疗方法、依药物类别、依给药途径、依最终使用者、按地区

Barth Syndrome Treatment Market, By Therapeutic Approaches, By Drug Classes, By Route of Administration, By End User, By Geography

出版日期: | 出版商: Coherent Market Insights | 英文 160 Pages | 商品交期: 2-3个工作天内

价格
简介目录

预计2024年全球巴斯症候群治疗市场规模将达1,411亿美元,2024年至2031年年复合成长率(CAGR)为13.2%,预计2031年将达3,361.1亿美元。

报告范围 报告详情
基准年 2023年 2024年市场规模 1411亿美元
实际资料 2019年至2023年 预测期 从2024年到2031年
预测 2024-2031 年复合年增长率: 13.20% 2031年价值预测 3361.1亿美元
图:2024 年按地区分類的巴斯症候群治疗市场占有率(%)
巴斯症候群治疗市场-IMG1

近年来,全球巴斯氏症治疗市场经历了显着成长。巴斯症候群是一种罕见的遗传性疾病,影响男性骨骼和心肌。此疾病的确切原因是 TAZ 基因突变,影响粒线体功能并导致结构异常。目前这种疾病无法治疗方法,治疗重点是控制症状和改善生活品质。开发新型标靶治疗的研究活动的开展以及对罕见疾病的认识不断提高是预计在预测期内推动全球巴特氏症治疗市场成长的主要因素。

市场动态:

由于遗传病患病率上升、政府对罕见疾病研究的支持力度加大以及罕见疾病药物研发活动的活性化等因素,预计全球巴斯症候群治疗市场将在未来八年显着增长。增长。然而,治疗成本上涨、缺乏认证核可药以及患者诊断困难等挑战正在限制市场成长。另一方面,基因和细胞疗法的发展具有为巴特氏症候群提供新治疗选择的强大潜力,从而在未来几年为参与者提供利润丰厚的机会。产业和研究机构继续努力更好地了解病理学,将进一步扩大治疗选择并促进市场扩张。

本研究的主要特点

本报告详细分析了全球巴斯症候群治疗市场,包括以2023年为基准年的预测期(2024-2031年)的市场规模(十亿美元)和年复合成长率(CAGR%)。

它还揭示了各个细分市场的潜在商机,并说明了该市场有吸引力的投资提案矩阵。

它还提供了有关市场驱动因素、限制因素、机会、新产品发布和核准、市场趋势、区域前景、主要企业采取的竞争策略等的主要考察。

根据公司亮点、产品系列、主要亮点、绩效和策略等参数,介绍了全球巴斯综合症治疗市场的主要企业概况。

本研究涵盖的主要企业包括 Agios Pharmaceuticals, Inc.、Amicus Therapeutics, Inc. 和 Stealth BioTherapeutics Inc.。

该报告的见解使负责人和公司经营团队能够就未来的产品发布、升级、市场扩张和行销策略做出明智的决策。

全球巴斯综合症治疗市场报告迎合了该行业的各个相关人员,如投资者、供应商、产品製造商、经销商、新进业者和财务分析师。

透过用于分析全球巴斯综合症治疗市场的各种策略矩阵,将促进相关人员的决策。

目录

第一章 研究目的与前提

  • 研究目的
  • 先决条件
  • 简称

第二章 市场展望

  • 报告说明
    • 市场定义和范围
  • 执行摘要

第三章市场动态、法规与趋势分析

  • 市场动态
  • 影响分析
  • 主要亮点
  • 监管场景
  • 产品发布/核准
  • PEST分析
  • 波特分析
  • 併购场景

第四章全球巴斯症候群治疗市场,依治疗方法,2024-2031 年(十亿美元)

  • 酵素替代疗法
  • 基因治疗
  • 支持性护理
  • 干细胞疗法
  • 其他(小分子药物)

第五章全球巴斯症候群治疗市场,依药物类别,2024-2031 年(十亿美元)

  • 心磷脂前驱物
  • 抗氧化剂
  • 免疫调节剂
  • 抗生素
  • 食品补充品
  • 其他的

第六章 全球巴斯症候群治疗市场,依给药途径,2024-2031 年(十亿美元)

  • 口服
  • 静脉
  • 其他(肌内和局部)

第七章 全球巴斯症候群治疗市场,依最终使用者划分,2024-2031 年(十亿美元)

  • 医院
  • 专科诊所
  • 研究所
  • 其他的

第八章全球巴斯症候群治疗市场,按地区,2019-2031(十亿美元)

  • 北美洲
  • 美国
  • 加拿大
  • 拉丁美洲
  • 巴西
  • 阿根廷
  • 墨西哥
  • 其他拉丁美洲
  • 欧洲
  • 德国
  • 英国
  • 西班牙
  • 法国
  • 义大利
  • 俄罗斯
  • 其他欧洲国家
  • 亚太地区
  • 中国
  • 印度
  • 日本
  • 澳洲
  • 韩国
  • ASEAN
  • 其他亚太地区
  • 中东
  • 海湾合作委员会国家
  • 以色列
  • 其他中东地区
  • 非洲
  • 南非
  • 北非
  • 中部非洲

第9章 竞争格局

  • Amneal Pharmaceuticals
  • Boehringer Ingelheim
  • Merck & Co.
  • Abbott
  • B Braun
  • Integra LifeSciences
  • Johnson & Johnson
  • Medtronic
  • MicroPort Scientific
  • NuVasive
  • Orthofix
  • Perrigo Company
  • Stryker
  • Zimmer Biomet
  • Eli Lilly and Company
  • F. Hoffmann-La Roche
  • Mylan
  • Stealth BioTherapeutics
  • Sanofi
  • Pfizer

第10章分析师建议

第十一章 参考文献与调查方法

  • 参考
  • 调查方法
  • 关于出版商
简介目录
Product Code: CMI7307

The Global Barth Syndrome Treatment Market is estimated to be valued at USD 141.10 billion in 2024 and is expected to reach USD 336.11 billion by 2031, exhibiting a compound annual growth rate (CAGR) of 13.2% from 2024 to 2031.

Report Coverage Report Details
Base Year: 2023 Market Size in 2024: US$ 141.10 Bn
Historical Data for: 2019 To 2023 Forecast Period: 2024 To 2031
Forecast Period 2024 to 2031 CAGR: 13.20% 2031 Value Projection: US$ 336.11 Bn
Figure. Barth Syndrome Treatment Market Share (%), By Region, 2024
Barth Syndrome Treatment Market - IMG1

The global Barth syndrome treatment market has been witnessing significant growth in the recent years. Barth syndrome is a rare genetic disorder affecting skeletal and cardiac muscles in males. The exact cause of the disease is mutations in the TAZ gene affecting mitochondrial function and leading to structural abnormalities. Currently, there is no cure for the condition and treatment focuses on managing symptoms and improving quality of life. Increasing research activities for developing novel targeted therapies and growing awareness about rare diseases are some key factors expected to drive the growth of the global Barth syndrome treatment market during the forecast period.

Market Dynamics:

The global Barth syndrome treatment market is projected to witness notable growth over the next eight years owing to several factors such as rising incidence of genetic disorders, growing government support for rare disease research, and increasing R&D activities for orphan drugs development. However, high treatment cost, lack of approved drugs, and difficulty in patient diagnosis are some challenges restraining the market growth. Meanwhile, development of gene and cell therapies hold strong potential in offering new treatment options for Barth syndrome and thereby, present lucrative opportunities for players in the coming years. Continued efforts from industry and research organizations to better understand the pathophysiology would further expand the therapeutic options and foster the market expansion.

Key features of the study:

This report provides in-depth analysis of the global Barth syndrome treatment market, and provides market size (USD Billion) and compound annual growth rate (CAGR%) for the forecast period (2024-2031), considering 2023 as the base year

It elucidates potential revenue opportunities across different segments and explains attractive investment proposition matrices for this market

This study also provides key insights about market drivers, restraints, opportunities, new product launches or approval, market trends, regional outlook, and competitive strategies adopted by key players

It profiles key players in the global Barth syndrome treatment market based on the following parameters - company highlights, products portfolio, key highlights, financial performance, and strategies

Key companies covered as a part of this study include Agios Pharmaceuticals, Inc., Amicus Therapeutics, Inc., and Stealth BioTherapeutics Inc.

Insights from this report would allow marketers and the management authorities of the companies to make informed decisions regarding their future product launches, type up-gradation, market expansion, and marketing tactics

Global Barth syndrome treatment market report caters to various stakeholders in this industry including investors, suppliers, product manufacturers, distributors, new entrants, and financial analysts

Stakeholders would have ease in decision-making through various strategy matrices used in analyzing the global Barth syndrome treatment market.

Detailed Segmentation:

  • By Therapeutic Approaches Insights (Revenue, USD Bn, 2019 - 2031)
    • Enzyme Replacement Therapy
    • Gene Therapy
    • Supportive Care
    • Stem Cell Therapy
    • Others (Small Molecule Drugs)
  • By Drug Classes Insights (Revenue, USD Bn, 2019 - 2031)
    • Cardiolipin Precursors
    • Antioxidants
    • Immunomodulators
    • Antibiotics
    • Dietary Supplements
    • Others
  • By Route Of Administration Insights (Revenue, USD Bn, 2019 - 2031)
    • Oral
    • Intravenous
    • Others (Intramuscular and Topical)
  • By End user Insights (Revenue, USD Bn, 2019 - 2031)
    • Hospitals
    • Specialty Clinics
    • Research Institutions
    • Others
  • By Regional Insights (Revenue, USD Bn, 2019 - 2031)
    • North America
    • U.S.
    • Canada
    • Latin America
    • Brazil
    • Argentina
    • Mexico
    • Rest of Latin America
    • Europe
    • Germany
    • U.K.
    • Spain
    • France
    • Italy
    • Russia
    • Rest of Europe
    • Asia Pacific
    • China
    • India
    • Japan
    • Australia
    • South Korea
    • ASEAN
    • Rest of Asia Pacific
    • Middle East
    • GCC Countries
    • Israel
    • Rest of Middle East
    • Africa
    • South Africa
    • North Africa
    • Central Africa
  • Key Players Insights
    • Amneal Pharmaceuticals
    • Boehringer Ingelheim
    • Merck & Co.
    • Abbott
    • B Braun
    • Integra LifeSciences
    • Johnson & Johnson
    • Medtronic
    • MicroPort Scientific
    • NuVasive
    • Orthofix
    • Perrigo Company
    • Stryker
    • Zimmer Biomet
    • Eli Lilly and Company
    • F. Hoffmann-La Roche
    • Mylan
    • Stealth BioTherapeutics
    • Sanofi
    • Pfizer

Table of Contents

1. RESEARCH OBJECTIVES AND ASSUMPTIONS

  • Research Objectives
  • Assumptions
  • Abbreviations

2. MARKET PURVIEW

  • Report Description
    • Market Definition and Scope
  • Executive Summary
    • Global Barth Syndrome Treatment Market, By Therapeutic Approaches
    • Global Barth Syndrome Treatment Market, By Drug Classes
    • Global Barth Syndrome Treatment Market, By Route of Administration
    • Global Barth Syndrome Treatment Market, By End User
    • Global Barth Syndrome Treatment Market, By Region

3. MARKET DYNAMICS, REGULATIONS, AND TRENDS ANALYSIS

  • Market Dynamics
  • Impact Analysis
  • Key Highlights
  • Regulatory Scenario
  • Product Launches/Approvals
  • PEST Analysis
  • PORTER's Analysis
  • Merger and Acquisition Scenario

4. Global Barth Syndrome Treatment Market, By Therapeutic Approaches, 2024-2031, (USD Bn)

  • Introduction
    • Market Share Analysis, 2024 and 2031 (%)
    • Y-o-Y Growth Analysis, 2020 - 2031
    • Segment Trends
  • Enzyme Replacement Therapy
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Gene Therapy
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Supportive Care
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Stem Cell Therapy
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Others (Small Molecule Drugs)
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)

5. Global Barth Syndrome Treatment Market, By Drug Classes, 2024-2031, (USD Bn)

  • Introduction
    • Market Share Analysis, 2024 and 2031 (%)
    • Y-o-Y Growth Analysis, 2019 - 2031
    • Segment Trends
  • Cardiolipin Precursors
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Antioxidants
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Immunomodulators
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Antibiotics
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Dietary Supplements
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Others
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)

6. Global Barth Syndrome Treatment Market, By Route of Administration, 2024-2031, (USD Bn)

  • Introduction
    • Market Share Analysis, 2024 and 2031 (%)
    • Y-o-Y Growth Analysis, 2019 - 2031
    • Segment Trends
  • Oral
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Intravenous
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Others (Intramuscular and Topical)
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)

7. Global Barth Syndrome Treatment Market, By End-User, 2024-2031, (USD Bn)

  • Introduction
    • Market Share Analysis, 2024 and 2031 (%)
    • Y-o-Y Growth Analysis, 2019 - 2031
    • Segment Trends
  • Hospitals
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Specialty Clinics
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Research Institutions
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)
  • Others
    • Introduction
    • Market Size and Forecast, and Y-o-Y Growth, 2019-2031, (USD Bn)

8. Global Barth Syndrome Treatment Market, By Region, 2019 - 2031, Value (USD Bn)

  • Introduction
    • Market Share (%) Analysis, 2024,2027 & 2031, Value (USD Bn)
    • Market Y-o-Y Growth Analysis (%), 2019 - 2031, Value (USD Bn)
    • Regional Trends
  • North America
    • Introduction
    • Market Size and Forecast, By Therapeutic Approaches, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Drug Classes, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Route of Administration, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By End-User, 2019 - 2031, Value (USD Bn)
  • U.S.
  • Canada
  • Latin America
    • Introduction
    • Market Size and Forecast, By Therapeutic Approaches, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Drug Classes, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Route of Administration, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By End-User, 2019 - 2031, Value (USD Bn)
  • Brazil
  • Argentina
  • Mexico
  • Rest of Latin America
  • Europe
    • Introduction
    • Market Size and Forecast, By Therapeutic Approaches, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Drug Classes, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Route of Administration, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By End-User, 2019 - 2031, Value (USD Bn)
  • Germany
  • U.K.
  • Spain
  • France
  • Italy
  • Russia
  • Rest of Europe
  • Asia Pacific
    • Introduction
    • Market Size and Forecast, By Therapeutic Approaches, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Drug Classes, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Route of Administration, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By End-User, 2019 - 2031, Value (USD Bn)
  • China
  • India
  • Japan
  • Australia
  • South Korea
  • ASEAN
  • Rest of Asia Pacific
  • Middle East
    • Introduction
    • Market Size and Forecast, By Therapeutic Approaches, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Drug Classes, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Route of Administration, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By End-User, 2019 - 2031, Value (USD Bn)
  • GCC Countries
  • Israel
  • Rest of Middle East
  • Africa
    • Introduction
    • Market Size and Forecast, By Therapeutic Approaches, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Drug Classes, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By Route of Administration, 2019 - 2031, Value (USD Bn)
    • Market Size and Forecast, By End-User, 2019 - 2031, Value (USD Bn)
  • South Africa
  • North Africa
  • Central Africa

9. COMPETITIVE LANDSCAPE

  • Amneal Pharmaceuticals
    • Company Highlights
    • Product Portfolio
    • Key Developments
    • Financial Performance
    • Strategies
  • Boehringer Ingelheim
    • Company Highlights
    • Product Portfolio
    • Key Developments
    • Financial Performance
    • Strategies
  • Merck & Co.
    • Company Highlights
    • Product Portfolio
    • Key Developments
    • Financial Performance
    • Strategies
  • Abbott
    • Company Highlights
    • Product Portfolio
    • Key Developments
    • Financial Performance
    • Strategies
  • B Braun
    • Company Highlights
    • Product Portfolio
    • Key Developments
    • Financial Performance
    • Strategies
  • Integra LifeSciences
    • Company Highlights
    • Product Portfolio
    • Key Developments
    • Financial Performance
    • Strategies
  • Johnson & Johnson
  • Medtronic
  • MicroPort Scientific
  • NuVasive
  • Orthofix
  • Perrigo Company
  • Stryker
  • Zimmer Biomet
  • Eli Lilly and Company
  • F. Hoffmann-La Roche
  • Mylan
  • Stealth BioTherapeutics
  • Sanofi
  • Pfizer

10. Analyst Recommendations

  • Wheel of Fortune
  • Analyst View
  • Coherent Opportunity Map

11. References and Research Methodology

  • References
  • Research Methodology
  • About us