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脊髓性肌肉萎缩症市场：按类型、治疗方法、年龄层、给药途径、通路和地区划分

Spinal Muscular Atrophy Market, by Type, by Treatment, by Age Group, by Route of Administration, by Distribution Channel, and by Region - Size, Share, Outlook, and Opportunity Analysis, 2025 - 2032

出版日期: 2025年03月03日 | 出版商:

Coherent Market Insights | 英文 156 Pages | 商品交期: 2-3个工作天内

价格

简介目录

2025 年全球脊髓性肌肉萎缩症市场规模估计为 20.189 亿美元，预计到 2032 年将达到 48.989 亿美元，2025 年至 2032 年的年复合成长率（CAGR）为 13.5%。

报告范围		报告详细信息
基准年	2024	2025年的市场规模	20.189亿美元
效能数据	从2020年到2024年	预测期	2025年至2032年
预测期：2025-2032年复合年增长率：	13.50%	2032年价值预测	48.989亿美元

数字。 2025年脊髓性肌肉萎缩症各地区市场占有率（%）

脊髓性肌肉萎缩症 (SMA) 是一种影响週边神经系统、中枢神经系统和随意肌肉运动（骨骼肌）的遗传性疾病。 SMA 是肌肉性的，因为它主要影响那些不会接收神经细胞衝动的肌肉。萎缩是肌肉收缩的医学术语，当肌肉不再接受神经细胞的刺激时就会发生这种情况。 SMA 是运动神经元疾病，导致脊髓中称为运动神经元的神经细胞流失。它主要发生在婴儿和儿童中，但也可能发生在成人中。 SMA 患者遗传了两个异常（突变）或缺失的运动神经元存活 1 (SMN1) 基因副本。

市场动态

预计预测期内市场主要参与者推出的新产品将推动市场成长。例如，2021年8月，在日本营运的药厂中外製药株式会社宣布推出用于治疗脊髓性肌肉萎缩症（SMA）的Evrisdi干糖浆60毫克（通用名：risdiplam）。

此外，预计主要企业越来越多地采用合作和协作研究等无机策略将在预测期内推动市场成长。例如，2021年3月，全球SMA研究的主要资助机构脊髓性肌肉萎缩症基金会与美国製药公司PTC Therapeutics, Inc.达成新的合作，专注于开发新治疗方法和再生药物，以进一步推动SMA和其他神经肌肉疾病的科学研究。

本研究的主要特点

本报告对全球脊髓性肌肉萎缩症市场进行了详细分析，并以 2024 年为基准年，给出了预测期（2025-2032 年）的市场规模和年复合成长率（CAGR%）。
它还强调了各个领域的潜在商机，并说明了该市场的有吸引力的投资提案矩阵。
它还提供了有关市场驱动因素、限制因素、机会、新产品发布和核准、市场趋势、区域前景和主要企业采用的竞争策略的主要考察。
全球脊髓性肌肉萎缩症市场的主要企业是根据公司亮点、产品系列、关键亮点、财务表现和策略等参数进行的分析。
本报告的见解将使负责人和企业经营团队能够就未来的产品发布、新兴趋势、市场扩张和行销策略做出明智的决策。
全球脊髓性肌肉萎缩症市场报告针对该行业的各个相关人员，例如投资者、供应商、产品製造商、经销商、新进入者和金融分析师1。
可以透过用于分析全球脊髓性肌肉萎缩症市场的各种策略矩阵来促进相关人员的决策。

Report Coverage	Report Details
Base Year:	2024	Market Size in 2025:	USD 2,018.9 Mn
Historical Data for:	2020 To 2024	Forecast Period:	2025 To 2032
Forecast Period 2025 to 2032 CAGR:	13.50%	2032 Value Projection:	USD 4,898.9 Mn

Spinal muscular atrophy (SMA) is a genetic disease that affects the peripheral nervous system, central nervous system, and voluntary muscle movement (skeletal muscle). SMA is muscular since it primarily affects muscles, which do not receive impulses from the nerve cells. Atrophy is the medical term for shrinking, which is what muscles do when they are not stimulated by nerve cells. SMA is a motor neuron disease that includes the loss of nerve cells termed motor neurons in the spinal cord. It mostly affects infants and children but can also develop in adults. An individual with SMA inherits two copies of a faulty (mutated) or missing survival motor neuron 1 (SMN1) gene.

Market Dynamics

The increasing product launches by the key players in the market are expected to drive the market growth over the forecast period. For instance, in August 2021, Chugai Pharmaceutical Co., Ltd., a drug manufacturer operating in Japan, announced that it had launched Evrysdi Dry Syrup 60 mg (generic name: risdiplam) for the treatment of spinal muscular atrophy (SMA).

Moreover, the increasing adoption of inorganic strategies such as partnerships and collaborations by the key players is expected to drive the market growth over the forecast period. For instance, in March 2021, the Spinal Muscular Atrophy Foundation, the leading funder of SMA research worldwide, and PTC Therapeutics, Inc., a U.S. based pharmaceutical company, entered into a new collaboration focused on developing new treatments and regenerative medicine to further advance scientific research in SMA and other neuromuscular disorders.

Key features of the study:

This report provides in-depth analysis of the global spinal muscular atrophy market, and provides market size (US$ Million) and compound annual growth rate (CAGR%) for the forecast period (2025-2032), considering 2024 as the base year
It elucidates potential revenue opportunities across different segments and explains attractive investment proposition matrices for this market
This study also provides key insights about market drivers, restraints, opportunities, new product launches or approval, market trends, regional outlook, and competitive strategies adopted by key players
It profiles key players in the global spinal muscular atrophy market based on the following parameters - company highlights, products portfolio, key highlights, financial performance, and strategies
Key companies covered as a part of this study include Biogen, CYTOKINETICS, Hoffmann-La Roche Ltd, Genentech, Inc., PTC Therapeutics, Inc., Novartis AG, Ionis Pharmaceuticals, Chugai Pharmaceutical Co., Ltd., NMD PHARMA A/S, and Astellas Pharma Inc.
Insights from this report would allow marketers and the management authorities of the companies to make informed decisions regarding their future product launches, type up-gradation, market expansion, and marketing tactics
The global spinal muscular atrophy market report caters to various stakeholders in this industry including investors, suppliers, product manufacturers, distributors, new entrants, and financial analysts1
Stakeholders would have ease in decision-making through various strategy matrices used in analyzing the global spinal muscular atrophy market

Detailed Segmentation:

Global Spinal Muscular Atrophy Market, By Type:
- Type I
- Type II
- Type III
- Type IV
Global Spinal Muscular Atrophy Market, By Treatment:
- Gene Therapy
- Disease-modifying drugs
Global Spinal Muscular Atrophy Market, By Age Group:
- Infant
- Adult
Global Spinal Muscular Atrophy Market, By Route of Administration:
- Oral
- Injectables
Global Spinal Muscular Atrophy Market, By Distribution Channel:
- Hospital Pharmacies
- Retail Pharmacies
- Online Pharmacies
Global Spinal Muscular Atrophy Market, By Region:
- North America
- Latin America
- Europe
- Asia Pacific
- Middle East
- Africa
Company Profiles
- Biogen
- CYTOKINETICS
- Hoffmann-La Roche Ltd
- Genentech, Inc.
- PTC Therapeutics, Inc.
- Novartis AG
- Ionis Pharmaceuticals
- Chugai Pharmaceutical Co., Ltd.
- NMD PHARMA A/S
- Astellas Pharma Inc

1. Research Objectives and Assumptions

Research Objectives
Assumptions
Abbreviations

2. Market Purview

Report Description
- Market Definition and Scope
Executive Summary
- Market Snapshot, By Type
- Market Snapshot, By Treatment
- Market Snapshot, By Age
- Market Snapshot, By Route of Administration
- Market Snapshot, By Distribution Channel
- Market Snapshot, By Region
Coherent Opportunity Map (COM)

3. Market Dynamics, Regulations, and Trends Analysis

Market Dynamics
- Drivers
- Restraints
- Market Opportunities
Impact Analysis
Market Trends
Acquisitions and Partnerships Scenario
Technological Advancements
Regulatory Scenario
PEST Analysis
Product Launches

4. Global Spinal Muscular Atrophy Market- Impact of Coronavirus (Covid-19) Pandemic

Overall Impact
Government Initiatives
COVID-19 Impact on the market

5. Global Spinal Muscular Atrophy Market, By Type, 2020 - 2032, (US$ Million)

Overview
- Market Share Analysis, 2025 and 2032 (%)
- Y-o-Y Growth Analysis, 2021 - 2032
- Segment Trends
Type I
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Type II
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Type III
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Type IV
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)

6. Global Spinal Muscular Atrophy Market, By Treatment, 2020 - 2032, (US$ Million)

Overview
- Market Share Analysis, 2025 and 2032 (%)
- Y-o-Y Growth Analysis, 2021 - 2032
- Segment Trends
Gene Therapy
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Disease-modifying drugs
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)

7. Global Spinal Muscular Atrophy Market, By Age, 2020 - 2032, (US$ Million)

Overview
- Market Share Analysis, 2025 and 2032 (%)
- Y-o-Y Growth Analysis, 2021 - 2032
- Segment Trends
Infant
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Adult
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)

8. Global Spinal Muscular Atrophy Market, By Route of Administration, 2020 - 2032, (US$ Million)

Overview
- Market Share Analysis, 2025 and 2032 (%)
- Y-o-Y Growth Analysis, 2021 - 2032
- Segment Trends
Oral
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Injectables
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)

9. Global Spinal Muscular Atrophy Market, By Distribution Channel, 2020 - 2032, (US$ Million)

Overview
- Market Share Analysis, 2025 and 2032 (%)
- Y-o-Y Growth Analysis, 2021 - 2032
- Segment Trends
Hospital Pharmacies
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Retail Pharmacies
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)
Online Pharmacies
- Overview
- Market Size and Forecast, and Y-o-Y Growth, 2020-2032, (US$ Million)

10. Global Spinal Muscular Atrophy Market, By Region, 2020 - 2032, (US$ Million)

Introduction
- Market Share Analysis, By Region, 2025 and 2032 (%)
- Y-o-Y Growth Analysis, For Regions, 2021-2032
- Regional Trends
North America
- Introduction
- Market Size and Forecast, and Y-o-Y Growth, By Type, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Age, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Route of Administration, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Country, 2020 - 2032, (US$ Million)
  - U.S.
  - Canada
Latin America
- Introduction
- Market Size and Forecast, and Y-o-Y Growth, By Type, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Age, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Route of Administration, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Country, 2020 - 2032, (US$ Million)
  - Brazil
  - Mexico
  - Argentina
  - Rest of Latin America
Europe
- Introduction
- Market Size and Forecast, and Y-o-Y Growth, By Type, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Age, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Route of Administration, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Country, 2020 - 2032, (US$ Million)
  - UK
  - Germany
  - Italy
  - France
  - Spain
  - Russia
  - Rest of Europe
Asia Pacific
- Introduction
- Market Size and Forecast, and Y-o-Y Growth, By Type, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Age, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Route of Administration, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Country, 2020 - 2032, (US$ Million)
  - China
  - India
  - Japan
  - ASEAN
  - Australia
  - South Korea
  - Rest of Asia Pacific
Middle East
- Introduction
- Market Size and Forecast, and Y-o-Y Growth, By Type, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Age, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Route of Administration, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Country, 2020 - 2032, (US$ Million)
  - GCC
  - Israel
  - Rest of Middle East
Africa
- Introduction
- Market Size and Forecast, and Y-o-Y Growth, By Type, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Age, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Route of Administration, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2020 - 2032, (US$ Million)
- Market Size and Forecast, and Y-o-Y Growth, By Country/Region, 2020 - 2032, (US$ Million)
  - North Africa
  - Central Africa
  - South Africa

11. Competitive Landscape

Biogen
- Company Highlights
- Product Portfolio
- Key Highlights
- Financial Performance
- Market Strategies
CYTOKINETICS
F. Hoffmann-La Roche Ltd
Genentech, Inc.
PTC Therapeutics, Inc.
Novartis AG
Ionis Pharmaceuticals
Chugai Pharmaceutical Co., Ltd.
NMD PHARMA A/S
Astellas Pharma Inc.

12. Analyst Recommendation

Wheel of Fortune
Analyst View
Coherent Opportunity Map

13. Section

References
Research Methodology
About Us and Sales Contact

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License/价格

脊髓性肌肉萎缩症市场：按类型、治疗方法、年龄层、给药途径、通路和地区划分