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2024-2032 年庞贝氏症治疗市场(依治疗方法、给药途径、配销通路、适应症类型和地区)Pompe Disease Treatment Market by Treatment, Route of Administration, Distribution Channel, Indication Type, and Region 2024-2032 |
2023年,全球庞贝氏症治疗市场规模达到10亿美元。展望未来, IMARC Group预计到2032年市场规模将达到13亿美元,2024-2032年复合年增长率(CAGR)为2.58%。临床研究和试验数量的增加、ERT 的日益普及以及患有庞贝病的患者数量的增加是推动市场发展的一些关键因素。
庞贝氏症是一种遗传性疾病,由身体细胞中一种称为肝醣的复合糖积聚引起,会影响器官、组织和肌肉。它是由溶酶体酶酸性α-葡萄糖苷酶(GAA)缺乏引起的常染色体隐性肝醣储存症候群。它与肌肉无力、肝臟肿大、呼吸困难、听力问题、肺部感染、心律不整和体重减轻有关。可使用各种工具和测试进行诊断,包括肌电图、X 光和磁振造影 (MRI)。庞贝氏症可以透过药物、酵素替代疗法 (ERT)、底物减少疗法 (SRT)、伴侣高级替代疗法 (CART) 和注射来治疗,有助于改善生活品质。
个体中遗传异常的盛行率显着上升,患有庞贝氏症的患者数量也随之增加。再加上婴儿庞贝氏症的增加以及父母对新生儿健康的日益担忧,这是推动市场成长的关键因素之一。此外,越来越多的老年人口容易患上这些疾病,导致对庞贝氏症治疗的需求不断增加。此外,开发庞贝氏症新疗法的临床研究和试验数量不断增加,正在对市场产生正面影响。除此之外,人们对 ERT 治疗庞贝氏症的认识不断提高,有利于市场的成长。此外,人们对各种治疗方法的认识有所提高,包括干细胞移植、骨髓移植、化疗和免疫疗法,因为它们具有众多优点。再加上人们对 Lumizyme 等 ERT 治疗替代品易于获得的认识,正在为市场创造积极的前景。除此之外,越来越多地采用健康保险政策,为庞贝氏症治疗提供财政援助并最大限度地减少医疗支出。此外,许多国家的政府和非政府组织 (NGO) 正在采取措施,为所有人提供优质的医疗保健设施。加上诊断技术的显着改进,预计将为市场带来良好的前景。
The global Pompe disease treatment market size reached US$ 1.0 Billion in 2023. Looking forward, IMARC Group expects the market to reach US$ 1.3 Billion by 2032, exhibiting a growth rate (CAGR) of 2.58% during 2024-2032. The increasing number of clinical studies and trials, the rising popularity of ERT, and the growing number of patients suffering from Pompe disease represent some of the key factors driving the market.
Pompe disease is a genetic disorder caused by the buildup of a complex sugar known as glycogen in the cells of the body, which affects organs, tissues, and muscles. It is an autosomal recessive glycogen storage syndrome caused by the deficiency of lysosomal enzyme acid a-glucosidase (GAA). It is associated with weak muscles, enlarged liver, trouble breathing, hearing problem, lung infection, irregular heartbeat, and losing weight. It is diagnosed using various tools and tests, including electromyography, X-rays, and magnetic resonance imaging (MRI). Pompe disease can be treated using medications, enzyme replacement therapy (ERT), substrate reduction therapy (SRT), chaperone-advanced replacement therapy (CART), and injections, which aid in improving the quality of life.
There is a considerable rise in the prevalence of genetic abnormalities among individuals and an increase in the number of patients suffering from Pompe disease. This, coupled with the growing Pompe disease among infants and increasing concerns among parents about the health of their newborns, represents one of the key factors bolstering the growth of the market. Moreover, the growing geriatric population that is susceptible to developing these medical disorders is resulting in an increasing demand for Pompe disease treatment. In addition, the expanding number of clinical studies and trials to develop new treatments for Pompe disease is influencing the market positively. Apart from this, the rising awareness among people about ERT for curing Pompe disease is favoring the market growth. Furthermore, there is an increase in awareness about various treatments, including stem cell transplant, bone marrow transplantation, chemotherapy, and immunotherapy, on account of their numerous advantages. This, along with the awareness about the easy availability of ERT treatment alternatives like lumizyme, is creating a positive outlook for the market. Besides this, there is a rise in the adoption of health insurance policies that provide financial assistance and minimize healthcare expenditure for Pompe disease treatment. Additionally, governments and non-governmental organizations (NGOs) of numerous countries are undertaking measures to offer quality healthcare facilities that are accessible to all. This, along with significant improvements in the diagnostic technologies, is anticipated to provide a favorable outlook to the market.
IMARC Group provides an analysis of the key trends in each segment of the global Pompe disease treatment market, along with forecasts at the global, regional, and country level from 2024-2032. Our report has categorized the market based on treatment, route of administration, distribution channel, and indication type.
Enzyme Replacement Therapy (ERT)
Substrate Reduction Therapy (SRT)
Chaperone-Advanced Replacement Therapy (CART)
Others
The report has provided a detailed breakup and analysis of the Pompe disease treatment market based on the treatment. This includes enzyme replacement therapy (ERT), substrate reduction therapy (SRT), chaperone-advanced replacement therapy (CART), and others. According to the report, enzyme replacement therapy (ERT) represented the largest segment.
Oral
Intravenous
Others
A detailed breakup and analysis of the Pompe disease treatment market based on the route of administration has also been provided in the report. This includes oral, intravenous, and others.
Hospital and Clinics Pharmacies
Retail Pharmacies
Online Pharmacies
Others
A detailed breakup and analysis of the Pompe disease treatment market based on the distribution channel has also been provided in the report. This includes hospital and clinics, retail, and online pharmacies, and others. According to the report, hospital and clinics pharmacies accounted for the largest market share.
Infantile-Onset Pompe Disease (IOPD)
Classic Infantile Form
Non-Classic Infantile Form
Late-Onset Pompe Disease (LOPD)
Others
A detailed breakup and analysis of the Pompe disease treatment market based on the indication type has also been provided in the report. This includes infantile-onset Pompe disease (IOPD), classic infantile form, non-classic infantile form, late-onset Pompe disease (LOPD), and others. According to the report, late-onset Pompe disease (LOPD) accounted for the largest market share.
North America
United States
Canada
Asia Pacific
China
Japan
India
South Korea
Australia
Indonesia
Others
Europe
Germany
France
United Kingdom
Italy
Spain
Russia
Others
Latin America
Brazil
Mexico
Others
Middle East and Africa
The report has also provided a comprehensive analysis of all the major regional markets that include North America (the United States and Canada), Asia Pacific (China, Japan, India, South Korea, Australia, Indonesia, and others), Europe (Germany, France, the United Kingdom, Italy, Spain, Russia, and others), Latin America (Brazil, Mexico, and others), and the Middle East and Africa. According to the report, North America was the largest market for Pompe disease treatment. Some of the factors driving the North America Pompe disease treatment market included the growing awareness about various alternative treatments, increasing number of clinical studies and trials, and well-established healthcare facilities.
The report has also provided a comprehensive analysis of the competitive landscape in the global Pompe disease treatment market. Detailed profiles of all major companies have also been provided. Some of the companies covered include Amicus Therapeutics Inc., Audentes Therapeutics Inc. (Astellas US Holding Inc.), Oxyrane UK Limited, Sanofi S.A., Spark Therapeutics Inc, etc.
Kindly, note that this only represents a partial list of companies, and the complete list has been provided in the report