市场调查报告书
商品编码
1464907
Duchenne氏肌肉失养症治疗药物市场:按药物类型、给药方法和最终用途分类 - 全球预测 2024-2030Duchenne Muscular Dystrophy Drugs Market by Drug Type (Casimersen, Deflazacort, Delandistrogene Moxeparvovec), Administration Method (Oral, Parental), End-Use - Global Forecast 2024-2030 |
※ 本网页内容可能与最新版本有所差异。详细情况请与我们联繫。
Duchenne氏肌肉失养症治疗药物市场规模预计2023年为15.7亿美元,预计2024年将达17亿美元,2030年将达28亿美元,复合年增长率为8.61%。
Duchenne氏肌肉失养症(DMD) 治疗市场专注于专门用于治疗 DMD 的药品的销售、开拓和生产,DMD 是一种以进行性肌肉退化和肌无力为特征的遗传性疾病。基因研究的进步和对 DMD 基因基础了解的突破正在带来更有针对性和更有效的治疗方法,有助于市场扩张。全球医疗保健支出的增加正在改善 DMD 治疗的可近性并有助于市场扩张。政府和非营利组织的资金和倡议正在支持研究和开发工作,并促进将 DMD 治疗引入市场。对药物核准和市场引入的严格监管要求可能会延迟获得创新疗法的机会,并且是市场领域的一个挑战。此外,基因编辑技术的进步,如CRISPR/Cas9和其他基因编辑工具,为Duchenne氏肌肉失养症的治疗提供了可能性。根据个人基因谱量身定制的个人化医疗方法的开发有可能提高疗效并最大限度地减少副作用,从而为市场成长创造机会。
主要市场统计 | |
---|---|
基准年[2023] | 15.7亿美元 |
预测年份 [2024] | 17亿美元 |
预测年份 [2030] | 28亿美元 |
复合年增长率(%) | 8.61% |
药物类型:卡西默森越来越多地被偏好作为Duchenne氏肌肉失养症的标靶治疗
Casimersen 被核准用于治疗已确诊的外显子 45 跳跃突变的 DMD 患者。这种基于需求的卡迪默森偏好对于具有某些遗传倾向的患者至关重要,并提供了标靶治疗选择。无论特定的基因突变如何,地夫可特都能有效减缓 DMD 的进展并提高广大患者的肌肉力量。 Derandystrogen moxeparvovec (Roctavian) 基因疗法的目标患者是那些将从直接纠正导致 DMD 的基因缺陷的方法中受益的患者。 Eteplirsen (exondis51) 适用于因外显子 51 跳跃而确认 DMD 基因突变的 DMD 患者。 Golodirsen 满足小众病患小组的需求,并针对外显子 53 跳跃的特定基因突变提供标靶基因治疗。 Viltolarsen 被核准用于治疗外显子 53 跳跃的 DMD 患者,透过针对特定基因突变为受影响的患者提供精准医疗方法。
最终用途:门诊 DMD 治疗的采用率增加
门诊中心,也称为流动护理中心,为不需要住院的患者提供医疗服务。门诊中心因其便利性和成本效益而日益成为 DMD 等慢性疾病的常规检查、诊断和治疗的首选。居家照护设施是一个快速发展的领域,可满足患者在自己家中接受医疗保健服务的愿望,包括 DMD 药物治疗。居家照护在患者舒适的家中提供持续、个人化的 DMD 药物治疗和管理。
区域洞察
美国和加拿大是参与Duchenne氏肌肉失养症(DMD) 治疗药物开发的主要企业的重要区域。美洲地区的特点是消费者意识高、研发投入高、政府政策优惠。美国在突破性治疗方法的开发中占据关键地位,并已为创新的 DMD治疗方法申请了多项专利。加拿大展现了强而有力的政府支持和官民合作关係来促进市场成长。欧盟 (EU) 国家一直处于 DMD 药物开发监管支持的最前沿,并采取了多项倡议来支持研究和获得治疗。欧洲、中东和非洲地区的专利活动非常活跃,多个国家都对发现做出了贡献。中东地区市场规模虽小,但投资不断加大,认可度不断提高。非洲在医疗保健基础设施和治疗取得方面面临挑战,并透过国际伙伴关係和投资提供成长潜力。亚太地区,特别是中国、日本和印度,DMD 治疗市场正在显着成长。亚太地区国家的市场成长归功于意识的提高、政府措施和医疗基础设施的改善。亚太地区国家的研究和投资十分活跃,其中日本在创新治疗方法和专利申请方面处于领先地位。中国和印度正在迅速推进研究并提供具有成本效益的治疗方法,显着影响市场动态和客户购买行为。
FPNV定位矩阵
FPNV定位矩阵对于评估Duchenne氏肌肉失养症药物市场至关重要。我们检视与业务策略和产品满意度相关的关键指标,以对供应商进行全面评估。这种深入的分析使用户能够根据自己的要求做出明智的决策。根据评估,供应商被分为四个成功程度不同的像限:前沿(F)、探路者(P)、利基(N)和重要(V)。
市场占有率分析
市场占有率分析是一种综合工具,可以对Duchenne氏肌肉失养症治疗药物市场供应商的现状进行深入而深入的研究。全面比较和分析供应商在整体收益、基本客群和其他关键指标方面的贡献,以便更好地了解公司的绩效及其在争夺市场占有率时面临的挑战。此外,该分析还提供了对该行业竞争特征的宝贵见解,包括在研究基准年观察到的累积、分散主导地位和合併特征等因素。详细程度的提高使供应商能够做出更明智的决策并制定有效的策略,以获得市场竞争优势。
1. 市场渗透率:提供有关主要企业所服务的市场的全面资讯。
2. 市场开拓:我们深入研究利润丰厚的新兴市场,并分析其在成熟细分市场的渗透率。
3. 市场多元化:提供有关新产品发布、开拓地区、最新发展和投资的详细资讯。
4. 竞争评估和情报:对主要企业的市场占有率、策略、产品、认证、监管状况、专利状况和製造能力进行全面评估。
5. 产品开发与创新:提供对未来技术、研发活动和突破性产品开发的见解。
1.Duchenne氏肌肉失养症治疗药物市场规模及预测是多少?
2.Duchenne氏肌肉失养症治疗药物市场预测期内需要考虑投资的产品、细分市场、应用和领域有哪些?
3.Duchenne氏肌肉失养症治疗药物市场的技术趋势和法规结构是什么?
4.Duchenne氏肌肉失养症治疗药物市场主要供应商的市场占有率是多少?
5. 进入Duchenne氏肌肉失养症药物市场的合适型态和策略手段是什么?
[182 Pages Report] The Duchenne Muscular Dystrophy Drugs Market size was estimated at USD 1.57 billion in 2023 and expected to reach USD 1.70 billion in 2024, at a CAGR 8.61% to reach USD 2.80 billion by 2030.
The Duchenne muscular dystrophy (DMD) drugs market focuses on the sales, development, and production of pharmaceuticals specifically aimed at treating DMD, a genetic disorder characterized by progressive muscle degeneration and weakness. Advancements in genetic research and breakthroughs in understanding the genetic basis of DMD are leading to more targeted and effective treatments, contributing to the market expansion. Higher global healthcare expenditure enables better treatment access for DMD, contributing to market growth. Funding and initiatives by governments and non-profit organizations boost research and development efforts, enhancing the market adoption of DMD drugs. Stringent regulatory requirements for drug approval and market introduction may delay access to innovative treatments, posing challenges in the market space. Moreover, ongoing advancements in gene editing technologies such as CRISPR/Cas9 and other gene-editing tools offer potential for curative treatments of Duchenne muscular dystrophy. The development of personalized medicine approaches tailored to individual genetic profiles may improve efficacy and minimize side effects, generating opportunities for market growth.
KEY MARKET STATISTICS | |
---|---|
Base Year [2023] | USD 1.57 billion |
Estimated Year [2024] | USD 1.70 billion |
Forecast Year [2030] | USD 2.80 billion |
CAGR (%) | 8.61% |
Drug Type: Rising preference for casimersen for targeted treatment of Duchenne muscular dystrophy
Casimersen is approved for treating DMD in patients with a confirmed mutation due to exon 45 skipping. This need-based preference for casimersen is critical for patients with a specific genetic makeup, providing a targeted treatment option. Deflazacort ensures efficacy in delaying disease progression and improving muscle strength to slow the progression of DMD across a broad range of patients, regardless of their specific genetic mutation. Delandistrogene Moxeparvovec (Roctavian) gene therapy is designed for patients that benefit from a direct approach to correcting the gene defect responsible for DMD. Eteplirsen (Exondys 51) is preferred for DMD patients observing confirmed mutation of the DMD gene due to exon 51 skipping. Golodirsen meets the needs of a niche patient group, offering a targeted genetic treatment with a specific genetic mutation amenable to exon 53 skipping. Viltolarsen is approved for DMD patients amenable to exon 53 skipping that targets a specific genetic alteration, providing a precision medicine approach for affected patients.
End-Use: Increasing adoption of DMD drugs in ambulatory centers
Ambulatory centers, also known as outpatient care centers, provide medical services to patients that do not require hospital admission. Ambulatory center facilities have been increasingly preferred for routine check-ups, diagnosis, and the management of chronic conditions such as DMD due to their convenience and cost-effectiveness. Homecare settings represent a rapidly growing segment that caters to the preference for receiving healthcare services, including DMD drug treatments, in the patient's home. Homecare settings allow for continuous, personalized care and the administration of DMD medications in the comfort of the patient's home.
Regional Insights
In the Americas region, the United States and Canada are pivotal due to the strong presence of key players engaged in developing Duchenne Muscular Dystrophy (DMD) drugs. The Americas region is characterized by high consumer awareness, substantial investments in R&D, and favorable government policies. The United States holds a key position in developing breakthrough therapies and has several patents filed for innovative DMD treatments. Canada demonstrates strong governmental support and public-private partnerships, fostering growth in the market arena. The European Union countries are at the forefront regarding regulatory support for DMD drug development and have several initiatives supporting research and access to treatment. Patent activity is high in the EMEA region, with several countries contributing to discoveries. The Middle East region, although smaller in terms of market size, is witnessing increased investment and growing awareness. Africa faces challenges related to healthcare infrastructure and treatment access and shows potential for growth through international partnerships and investments. The Asia Pacific region, especially China, Japan, and India, has grown significantly in the DMD drugs market. The market growth in the APAC countries is attributed to increasing awareness, governmental initiatives, and improving healthcare infrastructure. Research and investment in APAC countries have been robust, with Japan leading in innovative therapies and patent filings. China and India are rapidly advancing in research and offering cost-effective treatments, significantly affecting market dynamics and customer purchasing behaviors.
FPNV Positioning Matrix
The FPNV Positioning Matrix is pivotal in evaluating the Duchenne Muscular Dystrophy Drugs Market. It offers a comprehensive assessment of vendors, examining key metrics related to Business Strategy and Product Satisfaction. This in-depth analysis empowers users to make well-informed decisions aligned with their requirements. Based on the evaluation, the vendors are then categorized into four distinct quadrants representing varying levels of success: Forefront (F), Pathfinder (P), Niche (N), or Vital (V).
Market Share Analysis
The Market Share Analysis is a comprehensive tool that provides an insightful and in-depth examination of the current state of vendors in the Duchenne Muscular Dystrophy Drugs Market. By meticulously comparing and analyzing vendor contributions in terms of overall revenue, customer base, and other key metrics, we can offer companies a greater understanding of their performance and the challenges they face when competing for market share. Additionally, this analysis provides valuable insights into the competitive nature of the sector, including factors such as accumulation, fragmentation dominance, and amalgamation traits observed over the base year period studied. With this expanded level of detail, vendors can make more informed decisions and devise effective strategies to gain a competitive edge in the market.
Key Company Profiles
The report delves into recent significant developments in the Duchenne Muscular Dystrophy Drugs Market, highlighting leading vendors and their innovative profiles. These include Anuh Pharma Limited, Arlak Biotech Pvt.Ltd., Aurigene Pharmaceutical Services Ltd., Bayer Pharmaceutical, Cipla Inc., Enomark, Glasier Wellness, Inc., GlaxoSmithKline PLC, Johnson & Johnson Services, Inc., Leo Pharma, Lifecare Neuro Products Limited, Mankind Pharma Ltd., Merck & Co., Inc.,, MODASA Pharmaceuticals Pvt. Ltd., Novartis AG, Pfizer Inc., QndQ Derma, RayBiotech, Inc., Ronyd Healthcare Pvt Ltd., Sarepta Therapeutics, Inc., Sumitomo Corporation, Texas Pharmaceuticals Pvt. Ltd., Wallace Pharmaceuticals Pvt Ltd., Wellona Pharma, and Zuventus Healthcare Ltd..
Market Segmentation & Coverage
1. Market Penetration: It presents comprehensive information on the market provided by key players.
2. Market Development: It delves deep into lucrative emerging markets and analyzes the penetration across mature market segments.
3. Market Diversification: It provides detailed information on new product launches, untapped geographic regions, recent developments, and investments.
4. Competitive Assessment & Intelligence: It conducts an exhaustive assessment of market shares, strategies, products, certifications, regulatory approvals, patent landscape, and manufacturing capabilities of the leading players.
5. Product Development & Innovation: It offers intelligent insights on future technologies, R&D activities, and breakthrough product developments.
1. What is the market size and forecast of the Duchenne Muscular Dystrophy Drugs Market?
2. Which products, segments, applications, and areas should one consider investing in over the forecast period in the Duchenne Muscular Dystrophy Drugs Market?
3. What are the technology trends and regulatory frameworks in the Duchenne Muscular Dystrophy Drugs Market?
4. What is the market share of the leading vendors in the Duchenne Muscular Dystrophy Drugs Market?
5. Which modes and strategic moves are suitable for entering the Duchenne Muscular Dystrophy Drugs Market?