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市场调查报告书
商品编码
1786775

溶小体储积症治疗的全球市场，规模，占有率，趋势，产业分析报告:各疾病类型，各治疗类型，各终端用户，各地区 - 市场预测，2025年～2034年

Lysosomal Storage Disease Treatment Market Size, Share, Trends, & Industry Analysis Report By Disease Type, By Type of Therapy, By End User, and By Region - Market Forecast, 2025-2034
出版日期: | 出版商: Polaris Market Research | 英文 129 Pages | 商品交期: 最快1-2个工作天内

价格

根据 Polaris Market Research 的最新研究，溶小体贮积症治疗市场预计到 2034 年将达到 68 亿美元。本研究报告深入分析了当前的市场动态，并分析了未来的市场成长。

随着製药公司和研发机构开发针对罕见遗传疾病的新疗法，溶小体贮积症治疗市场正在稳步发展。认知度的提高、患者权益的增强以及支持性监管框架的完善，有助于加快药物审批，并改善创新疗法的可及性。

生物技术和个人化医疗投资的不断增加，正在将市场重点从对症治疗转向长期疾病管理和潜在治癒方法的开发。这一发展反映了人们对改善患者预后以及为戈谢氏症、法布瑞氏症和庞贝氏症等疾病提供更有效、更有针对性的治疗方案的强烈追求。

溶小体贮积症治疗市场报告重点

按疾病类型划分，戈谢氏症将在2024年占市场主导地位，这得益于其在全球的广泛流行和成熟的治疗生态系统。

按治疗类型划分，酵素替代疗法 (ERT) 细分市场在2024年占市场主导地位，这得益于其在各种溶酶体贮积症治疗中的应用日益广泛。

依最终用户划分，提供酵素替代疗法和干细胞治疗等专业介入措施的医院细分市场在2024年占市场主导地位。

受强劲的…推动，北美占了全球溶小体贮积症治疗市场的大部分占有率，2024年市场占有率达到36.98%。生物技术和製药公司正在开发治疗罕见遗传疾病的药物。

亚太地区占了 6.13% 的市场占有率，这得益于医疗保健基础设施的持续改善和先进诊断能力的普及。

全球主要市场参与者包括 Alexion Pharmaceuticals, Inc.、Amicus Therapeutics, Inc.、BioMarin Pharmaceutical Inc.、礼来公司、强生公司（Actelion Pharmaceuticals Ltd.）、默克公司、诺华公司、辉田公司、赛诺菲公司（健赞公司）、Sigilon Therapeutics, Inc. S.p.A.、Orphazyme A/S、Protalix BioTherapeutics, Inc. 和 Ultragenyx Pharmaceutical Inc.

目录

第1章 简介

第2章 摘要整理

第3章 调查手法

第4章 全球溶小体储积症治疗市场洞察

  • 市场概述
  • 溶小体储积症治疗市场动态
    • 促进因素和机会
      • 罕见遗传疾病发生率上升
      • 酵素替代疗法 (ERT) 的进展
    • 限制与课题
      • 治疗费用高且报销有限
  • PESTEL分析
  • 溶小体储积症治疗市场趋势
  • 价值链分析

第5章 全球溶小体储积症治疗市场:各疾病类型

  • 主要调查结果
  • 简介
  • 高雪氏症
  • 法布瑞氏症
  • 庞贝氏症
  • 黏多醣症
  • 其他

第6章 全球溶小体储积症治疗市场:各治疗类型

  • 主要调查结果
  • 简介
  • 酵素补充疗法
  • 干细胞疗法
  • 基材还原疗法
  • 其他

第7章 全球溶小体储积症治疗市场:各终端用户

  • 主要调查结果
  • 简介
  • 医院
  • 诊所
  • 其他

第8章 全球溶小体储积症治疗市场:各地区

  • 主要调查结果
  • 简介
    • 溶小体储积症治疗市场评估:各地区，2020-2034年
  • 北美
    • 北美:各疾病类型，2020～2034年
    • 北美:各治疗类型，2020年～2034年
    • 北美:各终端用户，2020～2034年
    • 美国
    • 加拿大
  • 欧洲
    • 欧洲:各疾病类型，2020～2034年
    • 欧洲:各治疗类型，2020～2034年
    • 欧洲:各终端用户，2020～2034年
    • 英国
    • 法国
    • 德国
    • 义大利
    • 西班牙
    • 荷兰
    • 俄罗斯
    • 其他欧洲
  • 亚太地区
    • 亚太地区:疾病各类型，2020～2034年
    • 亚太地区:各治疗类型，2020年～2034年
    • 亚太地区:各终端用户，2020～2034年
    • 中国
    • 印度
    • 马来西亚
    • 日本
    • 印尼
    • 韩国
    • 澳洲
    • 其他亚太地区
  • 中东·非洲
    • 中东·非洲:疾病各类型，2020～2034年
    • 中东·非洲:各治疗类型，2020～2034年
    • 中东·非洲:各终端用户，2020～2034年
    • 沙乌地阿拉伯
    • 阿拉伯联合大公国
    • 以色列
    • 南非
    • 其他中东·非洲
  • 南美
    • 南美:疾病各类型，2020-2034年
    • 南美:各治疗类型，2020-2034年
    • 南美:各终端用户，2020～2034年
    • 墨西哥
    • 巴西
    • 阿根廷
    • 其他南美国家

第9章 竞争情形

  • 扩大和收购的分析
    • 扩大
    • 收购
  • 联盟/合作/协定/公开

第10章 企业简介

  • Alexion Pharmaceuticals, Inc.
  • Amicus Therapeutics, Inc.
  • BioMarin Pharmaceutical Inc.
  • Eli Lilly and Company
  • Johnson & Johnson(Actelion Pharmaceuticals Ltd.)
  • Merck & Co., Inc.
  • Novartis AG
  • Pfizer Inc.
  • Sanofi(Genzyme Corporation)
  • Sigilon Therapeutics, Inc.
  • Takeda Pharmaceutical Company Limited(Shire Plc)
  • Chiesi Farmaceutici S.p.A.
Product Code: PM6066

The lysosomal storage disease treatment market size is expected to reach USD 6.80 Billion by 2034, according to a new study by Polaris Market Research. The report "Lysosomal Storage Disease Treatment Market Size, Share, Trends, & Industry Analysis Report By Disease Type (Gaucher's Diseases, Fabry Diseases, Pompe's Syndrome, Mucopolysaccharidosis, and Others), By Type of Therapy, By End User, and By Region - Market Forecast, 2025-2034" gives a detailed insight into current market dynamics and provides analysis on future market growth.

The lysosomal storage disease (LSD) treatment market is witnessing steady progress as pharmaceutical companies and research institutions develop new therapies aimed at addressing rare genetic disorders. Growing awareness, increasing patient advocacy, and supportive regulatory frameworks are helping accelerate drug approvals and improve access to innovative treatments.

Rising investments in biotechnology and personalized medicine are shifting the market focus beyond symptom control toward long-term disease management and the development of potential cures. This evolution reflects a strong push toward improving patient outcomes and delivering more effective, targeted therapies for conditions such as Gaucher disease, Fabry disease, and Pompe disease.

Lysosomal Storage Disease Treatment Market Report Highlights

Based on disease type, gaucher's disease segment dominated the market in 2024, driven by its wider global prevalence and the presence of an established therapeutic ecosystem.

In terms of type of therapy, the enzyme replacement therapy (ERT) segment dominated the market in 2024. This is driven by the increasing adoption in managing various lysosomal storage disorders.

In terms of end user, the hospital segment dominated the market in 2024, attributed to delivery of specialized interventions such as enzyme replacement therapies and stem cell-based procedures.

North America accounted for the majority share of 36.98 in the global lysosomal storage disease treatment market in 2024, due to the strong presence of biotech and pharmaceutical firms advancing treatments for rare genetic conditions.

Asia Pacific held 6.13% market share, owing to ongoing improvements in healthcare infrastructure and access to advanced diagnostic capabilities.

A few global key market players include Alexion Pharmaceuticals, Inc., Amicus Therapeutics, Inc., BioMarin Pharmaceutical Inc., Eli Lilly and Company, Johnson & Johnson (Actelion Pharmaceuticals Ltd.), Merck & Co., Inc., Novartis AG, Pfizer Inc., Sanofi (Genzyme Corporation), Sigilon Therapeutics, Inc., Takeda Pharmaceutical Company Limited (Shire Plc), Chiesi Farmaceutici S.p.A., Orphazyme A/S, Protalix BioTherapeutics, Inc., and Ultragenyx Pharmaceutical Inc.

Polaris Market Research has segmented the market report on the basis of disease type, type of therapy, end user, and region:

By Disease Type Outlook (Revenue, USD Billion, 2020-2034)

Gaucher's Diseases

Fabry Diseases

Pompe's Syndrome

Mucopolysaccharidosis

Others

By Type of Therapy Outlook (Revenue, USD Billion, 2020-2034)

Enzyme Replacement Therapy

Stem Cell Therapy

Substrate Reduction Therapy

Others

By End User Outlook (Revenue, USD Billion, 2020-2034)

Hospitals

Clinics

Others

By Regional Outlook (Revenue, USD Billion, 2020-2034)

North America

US

Canada

Europe

Germany

France

UK

Italy

Spain

Netherlands

Russia

Rest of Europe

Asia Pacific

China

Japan

India

Malaysia

South Korea

Indonesia

Australia

Vietnam

Rest of Asia Pacific

Middle East & Africa

Saudi Arabia

UAE

Israel

South Africa

Rest of Middle East & Africa

Latin America

Mexico

Brazil

Argentina

Rest of Latin America

Table of Contents

1. Introduction

  • 1.1. Report Description
    • 1.1.1. Objectives of the Study
    • 1.1.2. Market Scope
    • 1.1.3. Assumptions
  • 1.2. Stakeholders

2. Executive Summary

  • 2.1. Market Highlights

3. Research Methodology

  • 3.1. Overview
    • 3.1.1. Data Mining
  • 3.2. Data Sources
    • 3.2.1. Primary Sources
    • 3.2.2. Secondary Sources

4. Global Lysosomal Storage Disease Treatment Market Insights

  • 4.1. Lysosomal Storage Disease Treatment Market - Market Snapshot
  • 4.2. Lysosomal Storage Disease Treatment Market Dynamics
    • 4.2.1. Drivers and Opportunities
      • 4.2.1.1. Rising Incidence of Rare Genetic Disorders
      • 4.2.1.2. Advancements in Enzyme Replacement Therapy (ERT)
    • 4.2.2. Restraints and Challenges
      • 4.2.2.1. High Treatment Costs and Limited Reimbursement
  • 4.3. Porter's Five Forces Analysis
    • 4.3.1. Bargaining Power of Suppliers (Moderate)
    • 4.3.2. Threats of New Entrants: (Low)
    • 4.3.3. Bargaining Power of Buyers (Moderate)
    • 4.3.4. Threat of Substitute (Moderate)
    • 4.3.5. Rivalry among existing firms (High)
  • 4.4. PESTEL Analysis
  • 4.5. Lysosomal Storage Disease Treatment Market Trends
  • 4.6. Value Chain Analysis

5. Global Lysosomal Storage Disease Treatment Market, by Disease Type

  • 5.1. Key Findings
  • 5.2. Introduction
    • 5.2.1. Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • 5.3. Gaucher's Diseases
    • 5.3.1. Global Lysosomal Storage Disease Treatment Market, by Gaucher's Diseases, by Region, 2020-2034 (USD Billion)
  • 5.4. Fabry Diseases
    • 5.4.1. Global Lysosomal Storage Disease Treatment Market, by Fabry Diseases, by Region, 2020-2034 (USD Billion)
  • 5.5. Pompe's Syndrome
    • 5.5.1. Global Lysosomal Storage Disease Treatment Market, by Pompe's Syndrome, by Region, 2020-2034 (USD Billion)
  • 5.6. Mucopolysaccharidosis
    • 5.6.1. Global Lysosomal Storage Disease Treatment Market, by Mucopolysaccharidosis, by Region, 2020-2034 (USD Billion)
  • 5.7. Others
    • 5.7.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

6. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy

  • 6.1. Key Findings
  • 6.2. Introduction
    • 6.2.1. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • 6.3. Enzyme Replacement Therapy
    • 6.3.1. Global Lysosomal Storage Disease Treatment Market, by Enzyme Replacement Therapy, by Region, 2020-2034 (USD Billion)
  • 6.4. Stem Cell Therapy
    • 6.4.1. Global Lysosomal Storage Disease Treatment Market, by Stem Cell Therapy, by Region, 2020-2034 (USD Billion)
  • 6.5. Substrate Reduction Therapy
    • 6.5.1. Global Lysosomal Storage Disease Treatment Market, by Substrate Reduction Therapy, by Region, 2020-2034 (USD Billion)
  • 6.6. Others
    • 6.6.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

7. Global Lysosomal Storage Disease Treatment Market, by End User

  • 7.1. Key Findings
  • 7.2. Introduction
    • 7.2.1. Global Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 7.3. Hospitals
    • 7.3.1. Global Lysosomal Storage Disease Treatment Market, by Hospitals, by Region, 2020-2034 (USD Billion)
  • 7.4. Clinics
    • 7.4.1. Global Lysosomal Storage Disease Treatment Market, by Clinics, by Region, 2020-2034 (USD Billion)
  • 7.5. Others
    • 7.5.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

8. Global Lysosomal Storage Disease Treatment Market, by Geography

  • 8.1. Key Findings
  • 8.2. Introduction
    • 8.2.1. Lysosomal Storage Disease Treatment Market Assessment, By Geography, 2020-2034 (USD Billion)
  • 8.3. Lysosomal Storage Disease Treatment Market - North America
    • 8.3.1. North America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.3.2. North America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.3.3. North America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.3.4. Lysosomal Storage Disease Treatment Market - U.S.
      • 8.3.4.1. U.S.: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.3.4.2. U.S.: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.3.4.3. U.S.: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.3.5. Lysosomal Storage Disease Treatment Market - Canada
      • 8.3.5.1. Canada: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.3.5.2. Canada: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.3.5.3. Canada: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.4. Lysosomal Storage Disease Treatment Market - Europe
    • 8.4.1. Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.4.2. Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.4.3. Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.4. Lysosomal Storage Disease Treatment Market - UK
      • 8.4.4.1. UK: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.4.2. UK: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.4.3. UK: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.5. Lysosomal Storage Disease Treatment Market - France
      • 8.4.5.1. France: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.5.2. France: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.5.3. France: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.6. Lysosomal Storage Disease Treatment Market - Germany
      • 8.4.6.1. Germany: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.6.2. Germany: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.6.3. Germany: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.7. Lysosomal Storage Disease Treatment Market - Italy
      • 8.4.7.1. Italy: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.7.2. Italy: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.7.3. Italy: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.8. Lysosomal Storage Disease Treatment Market - Spain
      • 8.4.8.1. Spain: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.8.2. Spain: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.8.3. Spain: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.9. Lysosomal Storage Disease Treatment Market - Netherlands
      • 8.4.9.1. Netherlands: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.9.2. Netherlands: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.9.3. Netherlands: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.10. Lysosomal Storage Disease Treatment Market - Russia
      • 8.4.10.1. Russia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.10.2. Russia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.10.3. Russia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.11. Lysosomal Storage Disease Treatment Market - Rest of Europe
      • 8.4.11.1. Rest of Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.11.2. Rest of Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.11.3. Rest of Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.5. Lysosomal Storage Disease Treatment Market - Asia Pacific
    • 8.5.1. Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.5.2. Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.5.3. Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.4. Lysosomal Storage Disease Treatment Market - China
      • 8.5.4.1. China: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.4.2. China: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.4.3. China: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.5. Lysosomal Storage Disease Treatment Market - India
      • 8.5.5.1. India: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.5.2. India: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.5.3. India: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.6. Lysosomal Storage Disease Treatment Market - Malaysia
      • 8.5.6.1. Malaysia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.6.2. Malaysia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.6.3. Malaysia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.7. Lysosomal Storage Disease Treatment Market - Japan
      • 8.5.7.1. Japan: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.7.2. Japan: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.7.3. Japan: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.8. Lysosomal Storage Disease Treatment Market - Indonesia
      • 8.5.8.1. Indonesia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.8.2. Indonesia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.8.3. Indonesia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.9. Lysosomal Storage Disease Treatment Market - South Korea
      • 8.5.9.1. South Korea: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.9.2. South Korea: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.9.3. South Korea: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.10. Lysosomal Storage Disease Treatment Market - Australia
      • 8.5.10.1. Australia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.10.2. Australia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.10.3. Australia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.11. Lysosomal Storage Disease Treatment Market - Rest of Asia Pacific
      • 8.5.11.1. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.11.2. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.11.3. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.6. Lysosomal Storage Disease Treatment Market - Middle East & Africa
    • 8.6.1. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.6.2. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.6.3. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.4. Lysosomal Storage Disease Treatment Market - Saudi Arabia
      • 8.6.4.1. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.4.2. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.4.3. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.5. Lysosomal Storage Disease Treatment Market - UAE
      • 8.6.5.1. UAE: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.5.2. UAE: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.5.3. UAE: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.6. Lysosomal Storage Disease Treatment Market - Israel
      • 8.6.6.1. Israel: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.6.2. Israel: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.6.3. Israel: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.7. Lysosomal Storage Disease Treatment Market - South Africa
      • 8.6.7.1. South Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.7.2. South Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.7.3. South Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.8. Lysosomal Storage Disease Treatment Market - Rest of Middle East & Africa
      • 8.6.8.1. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.8.2. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.8.3. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.7. Lysosomal Storage Disease Treatment Market - Latin America
    • 8.7.1. Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.7.2. Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.7.3. Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.4. Lysosomal Storage Disease Treatment Market - Mexico
      • 8.7.4.1. Mexico: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.4.2. Mexico: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.4.3. Mexico: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.5. Lysosomal Storage Disease Treatment Market - Brazil
      • 8.7.5.1. Brazil: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.5.2. Brazil: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.5.3. Brazil: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.6. Lysosomal Storage Disease Treatment Market - Argentina
      • 8.7.6.1. Argentina: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.6.2. Argentina: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.6.3. Argentina: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.7. Lysosomal Storage Disease Treatment Market - Rest of Latin America
      • 8.7.7.1. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.7.2. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.7.3. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)

9. Competitive Landscape

  • 9.1. Expansion and Acquisition Analysis
    • 9.1.1. Expansion
    • 9.1.2. Acquisitions
  • 9.2. Partnerships/Collaborations/Agreements/Exhibitions

10. Company Profiles

  • 10.1. Alexion Pharmaceuticals, Inc.
    • 10.1.1. Company Overview
    • 10.1.2. Financial Performance
    • 10.1.3. Disease Type Benchmarking
    • 10.1.4. Recent Development
  • 10.2. Amicus Therapeutics, Inc.
    • 10.2.1. Company Overview
    • 10.2.2. Financial Performance
    • 10.2.3. Disease Type Benchmarking
    • 10.2.4. Recent Development
  • 10.3. BioMarin Pharmaceutical Inc.
    • 10.3.1. Company Overview
    • 10.3.2. Financial Performance
    • 10.3.3. Disease Type Benchmarking
    • 10.3.4. Recent Development
  • 10.4. Eli Lilly and Company
    • 10.4.1. Company Overview
    • 10.4.2. Financial Performance
    • 10.4.3. Disease Type Benchmarking
    • 10.4.4. Recent Development
  • 10.5. Johnson & Johnson (Actelion Pharmaceuticals Ltd.)
    • 10.5.1. Company Overview
    • 10.5.2. Financial Performance
    • 10.5.3. Disease Type Benchmarking
    • 10.5.4. Recent Development
  • 10.6. Merck & Co., Inc.
    • 10.6.1. Company Overview
    • 10.6.2. Financial Performance
    • 10.6.3. Disease Type Benchmarking
    • 10.6.4. Recent Development
  • 10.7. Novartis AG
    • 10.7.1. Company Overview
    • 10.7.2. Financial Performance
    • 10.7.3. Disease Type Benchmarking
    • 10.7.4. Recent Development
  • 10.8. Pfizer Inc.
    • 10.8.1. Company Overview
    • 10.8.2. Financial Performance
    • 10.8.3. Disease Type Benchmarking
    • 10.8.4. Recent Development
  • 10.9. Sanofi (Genzyme Corporation)
    • 10.9.1. Company Overview
    • 10.9.2. Financial Performance
    • 10.9.3. Disease Type Benchmarking
    • 10.9.4. Recent Development
  • 10.10. Sigilon Therapeutics, Inc.
    • 10.10.1. Company Overview
    • 10.10.2. Financial Performance
    • 10.10.3. Disease Type Benchmarking
    • 10.10.4. Recent Development
  • 10.11. Takeda Pharmaceutical Company Limited (Shire Plc)
    • 10.11.1. Company Overview
    • 10.11.2. Financial Performance
    • 10.11.3. Disease Type Benchmarking
    • 10.11.4. Recent Development
  • 10.12. Chiesi Farmaceutici S.p.A.
    • 10.12.1. Company Overview
    • 10.12.2. Financial Performance
    • 10.12.3. Disease Type Benchmarking
    • 10.12.4. Recent Development

List of Tables:

  • Table 1 Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 2 Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 3 Global Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 4 North America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 5 North America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 6 North America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 7 U.S.: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 8 U.S.: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 9 U.S.: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 10 Canada: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 11 Canada: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 12 Canada: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 13 Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 14 Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 15 Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 16 UK: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 17 UK: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 18 UK: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 19 France: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 20 France: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 21 France: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 22 Germany: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 23 Germany: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 24 Germany: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 25 Italy: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 26 Italy: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 27 Italy: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 28 Spain: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 29 Spain: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 30 Spain: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 31 Netherlands: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 32 Netherlands: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 33 Netherlands: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 34 Russia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 35 Russia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 36 Russia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 37 Rest of Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 38 Rest of Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 39 Rest of Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 40 Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 41 Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 42 Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 43 China: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 44 China: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 45 China: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 46 India: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 47 India: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 48 India: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 49 Malaysia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 50 Malaysia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 51 Malaysia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 52 Japan: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 53 Japan: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 54 Japan: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 55 Indonesia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 56 Indonesia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 57 Indonesia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 58 South Korea: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 59 South Korea: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 60 South Korea: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 61 Australia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 62 Australia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 63 Australia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 64 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 65 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 66 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 67 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 68 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 69 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 70 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 71 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 72 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 73 UAE: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 74 UAE: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 75 UAE: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 76 Israel: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 77 Israel: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 78 Israel: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 79 South Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 80 South Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 81 South Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 82 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 83 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 84 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 85 Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 86 Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 87 Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 88 Mexico: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 89 Mexico: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 90 Mexico: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 91 Brazil: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 92 Brazil: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 93 Brazil: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 94 Argentina: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 95 Argentina: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 96 Argentina: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 97 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 98 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 99 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)

List of Figures:

  • Figure 1. Global Lysosomal Storage Disease Treatment Market, 2020-2034 (USD Billion)
  • Figure 2. Integrated Ecosystem
  • Figure 3. Research Methodology: Top-Down & Bottom-Up Price
  • Figure 4. Market by Geography
  • Figure 5. Porter's Five Forces
  • Figure 6. Market by Disease Type
  • Figure 7. Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2024 & 2034 (USD Billion)
  • Figure 8. Market by Type of Therapy
  • Figure 9. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2024 & 2034 (USD Billion)
  • Figure 10. Market by End User
  • Figure 11. Global Lysosomal Storage Disease Treatment Market, by End User, 2024 & 2034 (USD Billion)
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