市场调查报告书
商品编码
1119090
庞贝病全球市场规模调查,按给药途径,按治疗类型(底物减少疗法,酵素替代疗法,伴侣替代疗法,支持性护理),用户,地区预测 2022-2028Global Pompe Diseases Market Size study, by Route of Administration, By Treatment Type (Substrate Reduction Therapy, Enzyme Replacement Therapy, Chaperone-Advanced Replacement Therapy, Supportive Care), By End User and Regional Forecasts 2022-2028 |
2022-2028 年预测期间的 5%。
庞贝病是一种影响身体细胞中称为糖原的复杂碳水化合物积累的疾病。它是遗传遗传的,会导致一些组织和器官,尤其是肌肉,积累糖原并停止正常运作。据估计,美国每 40,000 人中就有 1 人患有庞贝病。市场增长由新药推出、长期疗法的持续采用以及酵素替代疗法领域的发展增加等关键因素推动。例如,根据 2021 年 11 月发表在 Journal of Molecules 上的一篇题为“Pharmacological Chaperone Therapy for Pompe disease”的论文,与 rhGAA 一起静脉内给药的酵素替代疗法(ERT)是 Pompe 病的唯一治疗方法。得到正式认可的。由于 ERT 的缺点,研究人员正在寻找新的治疗方法,这是美国食品和药物管理局批准的唯一药物。此外,2021 年 8 月,酵素替代疗法 Aval 葡萄糖甘酵素 Alfa 获得美国食品药品监督管理局 (FDA) 的批准,用于治疗 1 岁及以上的迟发性庞贝病。此外,针对庞贝病的新兴免疫疗法将在未来几年带来丰厚的市场机会。然而,高昂的治疗成本将阻碍 2022-2028 年预测期内的市场增长。
庞贝病全球市场研究考虑的主要地区是亚太地区、北美、欧洲、拉丁美洲和世界其他地区。由于新药的推出和研发支出的增加,北美在整体市场份额方面处于领先地位。然而,由于患者对罕见病的认识不断提高以及该地区庞贝病的患病率上升,预计亚太地区将增长最快。
本报告中包括的主要市场进入者是:
本研究的目的是确定近年来各个细分市场和国家/地区的市场规模,并预测未来八年的价值。本报告旨在捕捉所调查的每个地区和国家的行业的定性和定量方面。此外,它还提供了有关关键方面的详细信息,例如定义市场未来增长的驱动因素和挑战。此外,该报告还应纳入微观市场中可供利益相关者投资的可用机会,以及对竞争格局和主要参与者的应用产品的深入分析。市场的详细细分和子细分如下所述。
按给药途径:
口头
肠胃外给药
按治疗类型
底物减少疗法 (SRT)
酵素替代疗法 (ERT)
伴侣替代疗法 (CART)
支持性护理
按最终用户
医院
诊断中心
门诊手术中心
杂项
按地区
北美
美国
加拿大
欧洲
英国
德国
法国
西班牙
意大利
其他欧洲
亚太地区
中国
印度
日本
澳大利亚
韩国
其他亚太地区
拉丁美洲
巴西
墨西哥
世界其他地方
此外,本研究考虑的年份是:
实际年份 - 2018 年、2019 年、2020 年
2021 年基准年
预测期 - 2022 年 至 2028 年
本报告的目标受众是全球庞贝病市场。
主要咨询公司和顾问
大公司、中型公司、中小企业
风险投资
增值经销商 (VAR)
第三方知识提供者
投资银行家
投资者
Global Pompe Diseases Market is valued at approximately USD XXX million in 2021 and is anticipated to grow with a healthy growth rate of more than 4.5% over the forecast period 2022-2028. Pompe disease is a disorder affected by the buildup of a complex sugar called glycogen in the body's cells. It is inherited genetically, and the buildup of glycogen in some tissues and organs, especially muscles, makes them less able to operate normally. In the United States, one in 40,000 people have Pompe disease. The market growth is driven by key factors such as launch of novel drugs and the continued uptake of long-term therapies and increasing development in the field of enzyme replacement therapies. For instance, Enzyme replacement therapy (ERT), which involves giving rhGAA intravenously, is the only treatment for Pompe illness that has been approved, according to a paper titled "Pharmacological Chaperone Therapy for Pompe Disease" that was published in the Journal of Molecules in November 2021. Researchers are looking for novel treatments because of the shortcomings of ERT. which is the sole medication acknowledged by the US Food and Drug Administration. Furthermore, in August 2021, Enzyme Replacement therapy "Aval glucosidase Alfa" has been approved by United State of Food and Drug Administration, for the patient aged 1 year and older with late onset pompe disease. Moreover, emerging immunotherapeutic approaches for Pompe disease create lucrative opportunity for the market in upcoming years. However, high Treatment Cost impedes the growth of the market over the forecast period of 2022-2028
The key regions considered for the global Pompe Diseases Market study include Asia Pacific, North America, Europe, Latin America, and Rest of the World. North America is leading the overall market share owing to rising launches of novel drugs and growing research and development expenditure. However, Asia Pacific is expected to be the fastest growing region due to growing awareness among patients regarding rare disorders and increase in the prevalence of pompe disease in the region.
Major market players included in this report are:
Amicus Therapeutics
CENTOGENE AG
Valerion Therapeutics
Astellas Pharma
EpiVax, Inc
Oxyrane
Sanofi
AVROBIO, Inc.
Genethon
Sangamo Therapeutics
The objective of the study is to define market sizes of different segments & countries in recent years and to forecast the values to the coming eight years. The report is designed to incorporate both qualitative and quantitative aspects of the industry within each of the regions and countries involved in the study. Furthermore, the report also caters the detailed information about the crucial aspects such as driving factors & challenges which will define the future growth of the market. Additionally, the report shall also incorporate available opportunities in micro markets for stakeholders to invest along with the detailed analysis of competitive landscape and Application offerings of key players. The detailed segments and sub-segment of the market are explained below:
By Route of Administration:
Oral
Parenteral
By Treatment Type:
Substrate Reduction Therapy (SRT)
Enzyme Replacement Therapy (ERT)
Chaperone-Advanced Replacement Therapy (CART)
Supportive Care
By End User:
Hospitals
Diagnostic Centers
Ambulatory Surgical Centers
Others
By Region:
North America
U.S.
Canada
Europe
UK
Germany
France
Spain
Italy
ROE
Asia Pacific
China
India
Japan
Australia
South Korea
RoAPAC
Latin America
Brazil
Mexico
Rest of the World
Furthermore, years considered for the study are as follows:
Historical year - 2018, 2019, 2020
Base year - 2021
Forecast period - 2022 to 2028
Target Audience of the Global Pompe Diseases Market in Market Study:
Key Consulting Companies & Advisors
Large, medium-sized, and small enterprises
Venture capitalists
Value-Added Resellers (VARs)
Third-party knowledge providers
Investment bankers
Investors
List of figures